Transforming Pediatric Rare Disease Drug Development: Enhancing Clinical Trials and Regulatory Evidence With Virtual Patients. - Sips, Fianne; Virgolin, Marco; Pasculli, Giuseppe; Reali, Federico; Paris, Alessio; Janus, Annette; Godfrin, Yann; Röshammar, Daniel; Marchetti, Luca; Knöchel, Jane (CPT: Pharmacometrics & Systems Pharmacology, 2025)