Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes.
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| Title: | Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes. |
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| Authors: | Zafra‐Puerta, Luis1,2,3 (AUTHOR), Iglesias‐Cabeza, Nerea1 (AUTHOR), Sciaccaluga, Miriam3,4 (AUTHOR), Bellingacci, Laura5 (AUTHOR), Canonichesi, Jacopo5 (AUTHOR), Sánchez‐Martín, Gema1 (AUTHOR), Costa, Cinzia6 (AUTHOR), Sánchez, Marina P.1 (AUTHOR) msanchezg@fjd.es, Serratosa, José M.1 (AUTHOR) joseserratosa@me.com |
| Source: | Clinical & Translational Medicine. Nov2025, Vol. 15 Issue 11, p1-25. 25p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 189524909 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Zafra‐Puerta%2C+Luis%22">Zafra‐Puerta, Luis</searchLink><relatesTo>1,2,3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Iglesias‐Cabeza%2C+Nerea%22">Iglesias‐Cabeza, Nerea</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sciaccaluga%2C+Miriam%22">Sciaccaluga, Miriam</searchLink><relatesTo>3,4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Bellingacci%2C+Laura%22">Bellingacci, Laura</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Canonichesi%2C+Jacopo%22">Canonichesi, Jacopo</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sánchez‐Martín%2C+Gema%22">Sánchez‐Martín, Gema</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Costa%2C+Cinzia%22">Costa, Cinzia</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sánchez%2C+Marina+P%2E%22">Sánchez, Marina P.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> msanchezg@fjd.es</i><br /><searchLink fieldCode="AR" term="%22Serratosa%2C+José+M%2E%22">Serratosa, José M.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> joseserratosa@me.com</i> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Clinical+%26+Translational+Medicine%22">Clinical & Translational Medicine</searchLink>. Nov2025, Vol. 15 Issue 11, p1-25. 25p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=189524909 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1002/ctm2.70514 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 25 StartPage: 1 Titles: – TitleFull: Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Zafra‐Puerta, Luis – PersonEntity: Name: NameFull: Iglesias‐Cabeza, Nerea – PersonEntity: Name: NameFull: Sciaccaluga, Miriam – PersonEntity: Name: NameFull: Bellingacci, Laura – PersonEntity: Name: NameFull: Canonichesi, Jacopo – PersonEntity: Name: NameFull: Sánchez‐Martín, Gema – PersonEntity: Name: NameFull: Costa, Cinzia – PersonEntity: Name: NameFull: Sánchez, Marina P. – PersonEntity: Name: NameFull: Serratosa, José M. IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 11 Text: Nov2025 Type: published Y: 2025 Identifiers: – Type: issn-print Value: 20011326 Numbering: – Type: volume Value: 15 – Type: issue Value: 11 Titles: – TitleFull: Clinical & Translational Medicine Type: main |
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