Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.

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Title: Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.
Authors: Zafra-Puerta, Luis1,2 (AUTHOR), Iglesias-Cabeza, Nerea1,2 (AUTHOR), Sanz, Pascual3,4 (AUTHOR), García-Gimeno, María Adelaida4,5 (AUTHOR), Sánchez-Martín, Gema1,5 (AUTHOR), Sánchez, Marina P.1 (AUTHOR), Serratosa, José M.1,2 (AUTHOR)
Source: International Journal of Molecular Sciences. Dec2025, Vol. 26 Issue 24, p11930. 18p.
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  Data: Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.
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  Data: <searchLink fieldCode="AR" term="%22Zafra-Puerta%2C+Luis%22">Zafra-Puerta, Luis</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Iglesias-Cabeza%2C+Nerea%22">Iglesias-Cabeza, Nerea</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sanz%2C+Pascual%22">Sanz, Pascual</searchLink><relatesTo>3,4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22García-Gimeno%2C+María+Adelaida%22">García-Gimeno, María Adelaida</searchLink><relatesTo>4,5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sánchez-Martín%2C+Gema%22">Sánchez-Martín, Gema</searchLink><relatesTo>1,5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Sánchez%2C+Marina+P%2E%22">Sánchez, Marina P.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Serratosa%2C+José+M%2E%22">Serratosa, José M.</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)
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  Data: <searchLink fieldCode="JN" term="%22International+Journal+of+Molecular+Sciences%22">International Journal of Molecular Sciences</searchLink>. Dec2025, Vol. 26 Issue 24, p11930. 18p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=190470196
RecordInfo BibRecord:
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    Identifiers:
      – Type: doi
        Value: 10.3390/ijms262411930
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      – Code: eng
        Text: English
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        PageCount: 18
        StartPage: 11930
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      – TitleFull: Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.
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            NameFull: Zafra-Puerta, Luis
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            NameFull: Iglesias-Cabeza, Nerea
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            NameFull: Sanz, Pascual
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            NameFull: García-Gimeno, María Adelaida
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            NameFull: Sánchez-Martín, Gema
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            NameFull: Sánchez, Marina P.
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            NameFull: Serratosa, José M.
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              Text: Dec2025
              Type: published
              Y: 2025
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              Value: 26
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            – TitleFull: International Journal of Molecular Sciences
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