Miglustat as a Treatment for Adults with Tangier Disease Neuropathy: The MUSTANG N-of-1 Trial with 21 months Clinical Observation.

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Title: Miglustat as a Treatment for Adults with Tangier Disease Neuropathy: The MUSTANG N-of-1 Trial with 21 months Clinical Observation.
Authors: Cook, Andrew1,2 (AUTHOR), Stuart, Beth3 (AUTHOR), Ochoa-Ferraro, Antonio4 (AUTHOR), Condon, Nicola4 (AUTHOR), Lawrence, Megan1 (AUTHOR), Webley, Fran1 (AUTHOR), Wallom, Kerri-Lee5 (AUTHOR), Forbes, Claire1 (AUTHOR), Veeranna, Vishy4 (AUTHOR), Wanninayake, Subadra4 (AUTHOR), Oliver, Tom1 (AUTHOR), Davies, Nicholas4 (AUTHOR), Dawson, Charlotte4 (AUTHOR), Platt, Frances5 (AUTHOR), Hiwot, Tarekegn4,6 (AUTHOR) tarekegn.geberhiwot@uhb.nhs.uk
Source: Neurology & Therapy. Feb2026, Vol. 15 Issue 1, p447-456. 10p.
Database: Academic Search Ultimate
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Description
ISSN:21938253
DOI:10.1007/s40120-025-00843-6