Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes.
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| Title: | Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes. |
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| Authors: | Jiang, Xin1,2 (AUTHOR), Schaeffer, Laure3 (AUTHOR), Patni, Divya1 (AUTHOR), Russo, Tommaso1,4 (AUTHOR), Lee, Chao-Zong1,2 (AUTHOR), Aguilar, Corey1,2 (AUTHOR), Marques, Christine1 (AUTHOR), Jansen-West, Karen5 (AUTHOR), Hruska-Plochan, Marian6 (AUTHOR), Ray-Soni, Ananya1,2 (AUTHOR), Lim, Su Min1,2 (AUTHOR), Held, Aaron1 (AUTHOR), Yue, Mei5 (AUTHOR), Castellanos Otero, Paula5 (AUTHOR), Aryal, Sandeep1,2 (AUTHOR), Beaussant, Hortense D. A. M.1 (AUTHOR), Basu, Himanish7 (AUTHOR), Takakuwa, Hiro8 (AUTHOR), Daughrity, Lillian M.5 (AUTHOR), Ramesh, Nandini1,2 (AUTHOR) |
| Source: | Science. 2/5/2026, Vol. 391 Issue 6785, p1-17. 17p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 191379634 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Jiang%2C+Xin%22">Jiang, Xin</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Schaeffer%2C+Laure%22">Schaeffer, Laure</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Patni%2C+Divya%22">Patni, Divya</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Russo%2C+Tommaso%22">Russo, Tommaso</searchLink><relatesTo>1,4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Lee%2C+Chao-Zong%22">Lee, Chao-Zong</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Aguilar%2C+Corey%22">Aguilar, Corey</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Marques%2C+Christine%22">Marques, Christine</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Jansen-West%2C+Karen%22">Jansen-West, Karen</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Hruska-Plochan%2C+Marian%22">Hruska-Plochan, Marian</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Ray-Soni%2C+Ananya%22">Ray-Soni, Ananya</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Lim%2C+Su+Min%22">Lim, Su Min</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Held%2C+Aaron%22">Held, Aaron</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Yue%2C+Mei%22">Yue, Mei</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Castellanos+Otero%2C+Paula%22">Castellanos Otero, Paula</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Aryal%2C+Sandeep%22">Aryal, Sandeep</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Beaussant%2C+Hortense+D%2E+A%2E+M%2E%22">Beaussant, Hortense D. A. M.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Basu%2C+Himanish%22">Basu, Himanish</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Takakuwa%2C+Hiro%22">Takakuwa, Hiro</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Daughrity%2C+Lillian+M%2E%22">Daughrity, Lillian M.</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Ramesh%2C+Nandini%22">Ramesh, Nandini</searchLink><relatesTo>1,2</relatesTo> (AUTHOR) – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Science%22">Science</searchLink>. 2/5/2026, Vol. 391 Issue 6785, p1-17. 17p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=191379634 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1126/science.adv2600 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 17 StartPage: 1 Titles: – TitleFull: Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Jiang, Xin – PersonEntity: Name: NameFull: Schaeffer, Laure – PersonEntity: Name: NameFull: Patni, Divya – PersonEntity: Name: NameFull: Russo, Tommaso – PersonEntity: Name: NameFull: Lee, Chao-Zong – PersonEntity: Name: NameFull: Aguilar, Corey – PersonEntity: Name: NameFull: Marques, Christine – PersonEntity: Name: NameFull: Jansen-West, Karen – PersonEntity: Name: NameFull: Hruska-Plochan, Marian – PersonEntity: Name: NameFull: Ray-Soni, Ananya – PersonEntity: Name: NameFull: Lim, Su Min – PersonEntity: Name: NameFull: Held, Aaron – PersonEntity: Name: NameFull: Yue, Mei – PersonEntity: Name: NameFull: Castellanos Otero, Paula – PersonEntity: Name: NameFull: Aryal, Sandeep – PersonEntity: Name: NameFull: Beaussant, Hortense D. A. M. – PersonEntity: Name: NameFull: Basu, Himanish – PersonEntity: Name: NameFull: Takakuwa, Hiro – PersonEntity: Name: NameFull: Daughrity, Lillian M. – PersonEntity: Name: NameFull: Ramesh, Nandini IsPartOfRelationships: – BibEntity: Dates: – D: 05 M: 02 Text: 2/5/2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 00368075 Numbering: – Type: volume Value: 391 – Type: issue Value: 6785 Titles: – TitleFull: Science Type: main |
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