Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes.

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Title: Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes.
Authors: Jiang, Xin1,2 (AUTHOR), Schaeffer, Laure3 (AUTHOR), Patni, Divya1 (AUTHOR), Russo, Tommaso1,4 (AUTHOR), Lee, Chao-Zong1,2 (AUTHOR), Aguilar, Corey1,2 (AUTHOR), Marques, Christine1 (AUTHOR), Jansen-West, Karen5 (AUTHOR), Hruska-Plochan, Marian6 (AUTHOR), Ray-Soni, Ananya1,2 (AUTHOR), Lim, Su Min1,2 (AUTHOR), Held, Aaron1 (AUTHOR), Yue, Mei5 (AUTHOR), Castellanos Otero, Paula5 (AUTHOR), Aryal, Sandeep1,2 (AUTHOR), Beaussant, Hortense D. A. M.1 (AUTHOR), Basu, Himanish7 (AUTHOR), Takakuwa, Hiro8 (AUTHOR), Daughrity, Lillian M.5 (AUTHOR), Ramesh, Nandini1,2 (AUTHOR)
Source: Science. 2/5/2026, Vol. 391 Issue 6785, p1-17. 17p.
Database: Academic Search Ultimate
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  Data: Blocking RAN translation without altering repeat RNAs rescues C9ORF72-related ALS and FTD phenotypes.
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  Data: <searchLink fieldCode="JN" term="%22Science%22">Science</searchLink>. 2/5/2026, Vol. 391 Issue 6785, p1-17. 17p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=191379634
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              Text: 2/5/2026
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              Y: 2026
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