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Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients with Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial.

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Title: Two-Year Outcomes Following Delandistrogene Moxeparvovec Treatment in Ambulatory Patients with Duchenne Muscular Dystrophy: Phase 3 EMBARK Trial.
Authors: Mendell, Jerry R.1,2 (AUTHOR) JMendell@sarepta.com, Muntoni, Francesco3 (AUTHOR), McDonald, Craig M.4 (AUTHOR), Mercuri, Eugenio M.5 (AUTHOR), Ciafaloni, Emma6 (AUTHOR), Komaki, Hirofumi7 (AUTHOR), Leon-Astudillo, Carmen8 (AUTHOR), Nascimento, Andrés9 (AUTHOR), Proud, Crystal10 (AUTHOR), Schara-Schmidt, Ulrike11 (AUTHOR), Veerapandiyan, Aravindhan12 (AUTHOR), Zaidman, Craig M.13 (AUTHOR), Furgerson, Matthew2 (AUTHOR), Ding, Kai2 (AUTHOR), Singh, Preeti2 (AUTHOR), Potter, Rachael2 (AUTHOR), Asher, Damon R.2 (AUTHOR), Murphy, Alexander P.14 (AUTHOR), Reid, Carol14 (AUTHOR), Hooper, Gregory14 (AUTHOR)
Source: Neurology & Therapy. Apr2026, Vol. 15 Issue 2, p545-559. 15p.
Database: Academic Search Ultimate
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  Data: <searchLink fieldCode="JN" term="%22Neurology+%26+Therapy%22">Neurology & Therapy</searchLink>. Apr2026, Vol. 15 Issue 2, p545-559. 15p.
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              Text: Apr2026
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