Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I. - Santos, Hallana Souza; Poletto, Edina; Vera, Luisa Natalia Pimentel; Farinon, Mirian; Kubaski, Francyne; Carneiro, Paola Barcelos; Carniel, Willian da Silva; Giugliani, Roberto; Matte, Ursula; Teixeira, Helder Ferreira; Schuh, Roselena Silvestri; Baldo, Guilherme (Pharmaceutics, 2026)