Liver-Targeted AAV-DJ-hCBS Therapy Achieves Long-Term Correction of Metabolic Imbalance in CBS-Deficient Mice.
Saved in:
| Title: | Liver-Targeted AAV-DJ-hCBS Therapy Achieves Long-Term Correction of Metabolic Imbalance in CBS-Deficient Mice. |
|---|---|
| Authors: | Joschko, Christian P.1 (AUTHOR), Wang, Chih-Chieh2 (AUTHOR), van Buiten, Azuwerus1 (AUTHOR), Goris, Maaike1,2 (AUTHOR), Hoogstra-Berends, Femke1 (AUTHOR), Wang, Joy2 (AUTHOR), Bacurio, Jan Henric2 (AUTHOR), Chen, Yinxing2 (AUTHOR), Jia, Nannan2 (AUTHOR), Deng, June2 (AUTHOR), Hu, Shiliang2 (AUTHOR), Nacht, Mariana2 (AUTHOR), Chiocco, Matthew J.2 (AUTHOR), Henning, Robert H.1 (AUTHOR), Deelman, Leo E.1 (AUTHOR) l.e.deelman@umcg.nl |
| Source: | International Journal of Molecular Sciences. Apr2026, Vol. 27 Issue 7, p3338. 22p. |
| Database: | Academic Search Ultimate |
|
Full text is not displayed to guests.
Login for full access.
|
|
| FullText | Links: – Type: pdflink Text: Availability: 1 |
|---|---|
| Header | DbId: asn DbLabel: Academic Search Ultimate An: 192957737 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
| IllustrationInfo | |
| Items | – Name: Title Label: Title Group: Ti Data: Liver-Targeted AAV-DJ-hCBS Therapy Achieves Long-Term Correction of Metabolic Imbalance in CBS-Deficient Mice. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Joschko%2C+Christian+P%2E%22">Joschko, Christian P.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Wang%2C+Chih-Chieh%22">Wang, Chih-Chieh</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22van+Buiten%2C+Azuwerus%22">van Buiten, Azuwerus</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Goris%2C+Maaike%22">Goris, Maaike</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Hoogstra-Berends%2C+Femke%22">Hoogstra-Berends, Femke</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Wang%2C+Joy%22">Wang, Joy</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Bacurio%2C+Jan+Henric%22">Bacurio, Jan Henric</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Chen%2C+Yinxing%22">Chen, Yinxing</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Jia%2C+Nannan%22">Jia, Nannan</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Deng%2C+June%22">Deng, June</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Hu%2C+Shiliang%22">Hu, Shiliang</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Nacht%2C+Mariana%22">Nacht, Mariana</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Chiocco%2C+Matthew+J%2E%22">Chiocco, Matthew J.</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Henning%2C+Robert+H%2E%22">Henning, Robert H.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Deelman%2C+Leo+E%2E%22">Deelman, Leo E.</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> l.e.deelman@umcg.nl</i> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22International+Journal+of+Molecular+Sciences%22">International Journal of Molecular Sciences</searchLink>. Apr2026, Vol. 27 Issue 7, p3338. 22p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=192957737 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3390/ijms27073338 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 22 StartPage: 3338 Titles: – TitleFull: Liver-Targeted AAV-DJ-hCBS Therapy Achieves Long-Term Correction of Metabolic Imbalance in CBS-Deficient Mice. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Joschko, Christian P. – PersonEntity: Name: NameFull: Wang, Chih-Chieh – PersonEntity: Name: NameFull: van Buiten, Azuwerus – PersonEntity: Name: NameFull: Goris, Maaike – PersonEntity: Name: NameFull: Hoogstra-Berends, Femke – PersonEntity: Name: NameFull: Wang, Joy – PersonEntity: Name: NameFull: Bacurio, Jan Henric – PersonEntity: Name: NameFull: Chen, Yinxing – PersonEntity: Name: NameFull: Jia, Nannan – PersonEntity: Name: NameFull: Deng, June – PersonEntity: Name: NameFull: Hu, Shiliang – PersonEntity: Name: NameFull: Nacht, Mariana – PersonEntity: Name: NameFull: Chiocco, Matthew J. – PersonEntity: Name: NameFull: Henning, Robert H. – PersonEntity: Name: NameFull: Deelman, Leo E. IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 04 Text: Apr2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 16616596 Numbering: – Type: volume Value: 27 – Type: issue Value: 7 Titles: – TitleFull: International Journal of Molecular Sciences Type: main |
| ResultId | 1 |