Ethics and equity in access to disease‐modifying therapies and newborn screening for spinal muscular atrophy: A scoping review.

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Title: Ethics and equity in access to disease‐modifying therapies and newborn screening for spinal muscular atrophy: A scoping review.
Authors: Murugasen, Serini1 (AUTHOR) serini.murugasen@uct.ac.za, Kruger, Mariana2 (AUTHOR), Blockman, Marc3 (AUTHOR), Wilmshurst, Jo M.1,4 (AUTHOR)
Source: Developmental Medicine & Child Neurology. Apr2026, p1. 13p. 5 Illustrations.
Database: Academic Search Ultimate
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DbLabel: Academic Search Ultimate
An: 193342332
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PubType: Academic Journal
PubTypeId: academicJournal
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  Data: Ethics and equity in access to disease‐modifying therapies and newborn screening for spinal muscular atrophy: A scoping review.
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RecordInfo BibRecord:
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      – Type: doi
        Value: 10.1111/dmcn.70297
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      – Code: eng
        Text: English
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        PageCount: 13
        StartPage: 1
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      – TitleFull: Ethics and equity in access to disease‐modifying therapies and newborn screening for spinal muscular atrophy: A scoping review.
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            NameFull: Kruger, Mariana
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            NameFull: Blockman, Marc
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            NameFull: Wilmshurst, Jo M.
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            – D: 30
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              Text: Apr2026
              Type: published
              Y: 2026
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            – TitleFull: Developmental Medicine & Child Neurology
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