356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study.
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| Title: | 356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study. |
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| Authors: | Tard, C.1 (AUTHOR), Sacconi, S.1 (AUTHOR), Taouagh, N.1 (AUTHOR), Bouhour, F.1 (AUTHOR), Michaud, M.1 (AUTHOR), Beltran, S.1 (AUTHOR), Fournier, M.1 (AUTHOR), Demurger, F.1 (AUTHOR), Lagrange, E.1 (AUTHOR), Spinazzi, M.1 (AUTHOR), Noury, J.1 (AUTHOR), Magot, A.1 (AUTHOR), Cintas, P.1 (AUTHOR), Renard, D.1 (AUTHOR), Arrassi, A.1 (AUTHOR), Salort-Campana, E.1 (AUTHOR), Attarian, S.1 (AUTHOR), Laforet, P.1 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2025 Supplement, Vol. 53, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2025.106086 |
