356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study.
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| Title: | 356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study. |
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| Authors: | Tard, C.1 (AUTHOR), Sacconi, S.1 (AUTHOR), Taouagh, N.1 (AUTHOR), Bouhour, F.1 (AUTHOR), Michaud, M.1 (AUTHOR), Beltran, S.1 (AUTHOR), Fournier, M.1 (AUTHOR), Demurger, F.1 (AUTHOR), Lagrange, E.1 (AUTHOR), Spinazzi, M.1 (AUTHOR), Noury, J.1 (AUTHOR), Magot, A.1 (AUTHOR), Cintas, P.1 (AUTHOR), Renard, D.1 (AUTHOR), Arrassi, A.1 (AUTHOR), Salort-Campana, E.1 (AUTHOR), Attarian, S.1 (AUTHOR), Laforet, P.1 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2025 Supplement, Vol. 53, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 193863465 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=193863465 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.nmd.2025.106086 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 1 StartPage: N.PAG Titles: – TitleFull: 356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Tard, C. – PersonEntity: Name: NameFull: Sacconi, S. – PersonEntity: Name: NameFull: Taouagh, N. – PersonEntity: Name: NameFull: Bouhour, F. – PersonEntity: Name: NameFull: Michaud, M. – PersonEntity: Name: NameFull: Beltran, S. – PersonEntity: Name: NameFull: Fournier, M. – PersonEntity: Name: NameFull: Demurger, F. – PersonEntity: Name: NameFull: Lagrange, E. – PersonEntity: Name: NameFull: Spinazzi, M. – PersonEntity: Name: NameFull: Noury, J. – PersonEntity: Name: NameFull: Magot, A. – PersonEntity: Name: NameFull: Cintas, P. – PersonEntity: Name: NameFull: Renard, D. – PersonEntity: Name: NameFull: Arrassi, A. – PersonEntity: Name: NameFull: Salort-Campana, E. – PersonEntity: Name: NameFull: Attarian, S. – PersonEntity: Name: NameFull: Laforet, P. IsPartOfRelationships: – BibEntity: Dates: – D: 02 M: 09 Text: 2025 Supplement Type: published Y: 2025 Identifiers: – Type: issn-print Value: 09608966 Numbering: – Type: volume Value: 53 Titles: – TitleFull: Neuromuscular Disorders Type: main |
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