356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study.

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Title: 356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study.
Authors: Tard, C.1 (AUTHOR), Sacconi, S.1 (AUTHOR), Taouagh, N.1 (AUTHOR), Bouhour, F.1 (AUTHOR), Michaud, M.1 (AUTHOR), Beltran, S.1 (AUTHOR), Fournier, M.1 (AUTHOR), Demurger, F.1 (AUTHOR), Lagrange, E.1 (AUTHOR), Spinazzi, M.1 (AUTHOR), Noury, J.1 (AUTHOR), Magot, A.1 (AUTHOR), Cintas, P.1 (AUTHOR), Renard, D.1 (AUTHOR), Arrassi, A.1 (AUTHOR), Salort-Campana, E.1 (AUTHOR), Attarian, S.1 (AUTHOR), Laforet, P.1 (AUTHOR)
Source: Neuromuscular Disorders. 2025 Supplement, Vol. 53, pN.PAG-N.PAG. 1p.
Database: Academic Search Ultimate
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PubType: Academic Journal
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  Data: 356PReal-life effectiveness after switching to avalglucosidase alfa in late-onset Pompe disease patients worsening on alglucosidase alfa therapy: a French cohort study.
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  Data: <searchLink fieldCode="JN" term="%22Neuromuscular+Disorders%22">Neuromuscular Disorders</searchLink>. 2025 Supplement, Vol. 53, pN.PAG-N.PAG. 1p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=193863465
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        Value: 10.1016/j.nmd.2025.106086
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              Text: 2025 Supplement
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