Safety of Adeno-Associated Viral Vectors in Gene Therapy: Mechanisms of Toxicity, Clinical Risks, and Strategies for Their Minimization.

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Title: Safety of Adeno-Associated Viral Vectors in Gene Therapy: Mechanisms of Toxicity, Clinical Risks, and Strategies for Their Minimization.
Authors: Tsaregorodtseva, Tatiana S.1 (AUTHOR), Radyukhina, Maria A.1,2 (AUTHOR), Ayupova, Aisylu I.1,3 (AUTHOR), Solovyeva, Valeriya V.1,4 (AUTHOR), Sufianov, Albert A.2,3,5 (AUTHOR), Sufianova, Galina Z.1,4 (AUTHOR), Rizvanov, Albert A.1,2,5 (AUTHOR) albert.rizvanov@kpfu.ru
Source: International Journal of Molecular Sciences. Jun2026, Vol. 27 Issue 11, p4818. 31p.
Database: Academic Search Ultimate
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ISSN:16616596
DOI:10.3390/ijms27114818