Optimizing In Vitro Efficacy Assessment of the Antisense Oligonucleotide Nusinersen in Human Cellular Models.

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Title: Optimizing In Vitro Efficacy Assessment of the Antisense Oligonucleotide Nusinersen in Human Cellular Models.
Authors: Tisnikar, Maša Sinreih1 (AUTHOR), Zottel, Alja1,2 (AUTHOR), Kristan, Katja1,2 (AUTHOR) katja.kristan@sandoz.net, Lanišnik Rižner, Tea1,2 (AUTHOR) tea.lanisnik-rizner@mf.uni-lj.si
Source: Pharmaceutics. Jun2026, Vol. 18 Issue 6, p652. 18p.
Database: Academic Search Ultimate
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  Data: Optimizing In Vitro Efficacy Assessment of the Antisense Oligonucleotide Nusinersen in Human Cellular Models.
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  Data: <searchLink fieldCode="JN" term="%22Pharmaceutics%22">Pharmaceutics</searchLink>. Jun2026, Vol. 18 Issue 6, p652. 18p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=194907805
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        Value: 10.3390/pharmaceutics18060652
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        Text: English
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      – TitleFull: Optimizing In Vitro Efficacy Assessment of the Antisense Oligonucleotide Nusinersen in Human Cellular Models.
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              Text: Jun2026
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              Y: 2026
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