A Comprehensive Update on Pompe Disease: From Existing Therapies to Emerging Curative Strategies.

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Title: A Comprehensive Update on Pompe Disease: From Existing Therapies to Emerging Curative Strategies.
Authors: Estevez Barcia, Rebeca1 (AUTHOR), Colón, Cristóbal1,2 (AUTHOR), Hermida-Ameijeiras, Álvaro3 (AUTHOR), López-Valverde, Laura1,4 (AUTHOR), Rodrigues, Daniel1,2,5 (AUTHOR), Domínguez-González, Cristina4,6 (AUTHOR), Díaz-Manera, Jordi5,6,7 (AUTHOR), Couce, Maria L.1,2,3 (AUTHOR) maria.luz.couce.pico@sergas.es, Alvarez, José Victor1,2 (AUTHOR) jose.victor.alvarez.gonzalez@sergas.es
Source: International Journal of Molecular Sciences. Jul2026, Vol. 27 Issue 13, p5726. 25p.
Database: Academic Search Ultimate
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ISSN:16616596
DOI:10.3390/ijms27135726