Enzyme replacement therapy for mucopolysaccharidoses: opinions of patients and families.
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| Title: | Enzyme replacement therapy for mucopolysaccharidoses: opinions of patients and families. |
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| Authors: | Coman DJ; Bruce Lefroy Centre for Genetic Health Research, Murdoch Childrens Research Institute, Victoria, Australia., Hayes IM, Collins V, Sahhar M, Wraith JE, Delatycki MB |
| Source: | The Journal of pediatrics [J Pediatr] 2008 May; Vol. 152 (5), pp. 723-7. Date of Electronic Publication: 2008 Feb 20. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Mosby Country of Publication: United States NLM ID: 0375410 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1097-6833 (Electronic) Linking ISSN: 00223476 NLM ISO Abbreviation: J Pediatr Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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