Blockade of ActRIIB signaling triggers muscle fatigability and metabolic myopathy.

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Title: Blockade of ActRIIB signaling triggers muscle fatigability and metabolic myopathy.
Authors: Relizani K; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France., Mouisel E; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Current address: Inserm UMR 1048, Université Paul Sabatier, Toulouse, France., Giannesini B; Aix-Marseille Université, Centre National de la Recherche Scientifique, Centre de Resonance Magnetique Biologique et Medicale UMR 7339, Marseille, France., Hourdé C; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France., Patel K; School of Biological Sciences, University of Reading, Reading, UK., Morales Gonzalez S; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany., Jülich K; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany., Vignaud A; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Généthon, 1 bis rue de l'Internationale, Evry, France., Piétri-Rouxel F; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France., Fortin D; INSERM U 769, Université Paris-Sud, Châtenay-Malabry, France., Garcia L; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France., Blot S; Unité de Neurologie, Ecole Nationale Vétérinaire d'Alfort, Université Paris Est, Créteil, France., Ritvos O; Department of Bacteriology and Immunology, Haartman Institute, University of Helsinki, Helsinki, Finland., Bendahan D; Aix-Marseille Université, Centre National de la Recherche Scientifique, Centre de Resonance Magnetique Biologique et Medicale UMR 7339, Marseille, France., Ferry A; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Université Paris Descartes, Paris, France., Ventura-Clapier R; INSERM U 769, Université Paris-Sud, Châtenay-Malabry, France., Schuelke M; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany. Electronic address: markus.schuelke@charite.de., Amthor H; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France; Service Génétique Médicale, CHU Necker-Enfants Malades, Université Paris Descartes, Paris, France. Electronic address: helge.amthor@uvsq.fr.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2014 Aug; Vol. 22 (8), pp. 1423-1433. Date of Electronic Publication: 2014 May 27.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Blockade of ActRIIB signaling triggers muscle fatigability and metabolic myopathy.
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  Data: <searchLink fieldCode="AU" term="%22Relizani+K%22">Relizani K</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France.<br /><searchLink fieldCode="AU" term="%22Mouisel+E%22">Mouisel E</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Current address: Inserm UMR 1048, Université Paul Sabatier, Toulouse, France.<br /><searchLink fieldCode="AU" term="%22Giannesini+B%22">Giannesini B</searchLink>; Aix-Marseille Université, Centre National de la Recherche Scientifique, Centre de Resonance Magnetique Biologique et Medicale UMR 7339, Marseille, France.<br /><searchLink fieldCode="AU" term="%22Hourdé+C%22">Hourdé C</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France.<br /><searchLink fieldCode="AU" term="%22Patel+K%22">Patel K</searchLink>; School of Biological Sciences, University of Reading, Reading, UK.<br /><searchLink fieldCode="AU" term="%22Morales+Gonzalez+S%22">Morales Gonzalez S</searchLink>; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany.<br /><searchLink fieldCode="AU" term="%22Jülich+K%22">Jülich K</searchLink>; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany.<br /><searchLink fieldCode="AU" term="%22Vignaud+A%22">Vignaud A</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Généthon, 1 bis rue de l'Internationale, Evry, France.<br /><searchLink fieldCode="AU" term="%22Piétri-Rouxel+F%22">Piétri-Rouxel F</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France.<br /><searchLink fieldCode="AU" term="%22Fortin+D%22">Fortin D</searchLink>; INSERM U 769, Université Paris-Sud, Châtenay-Malabry, France.<br /><searchLink fieldCode="AU" term="%22Garcia+L%22">Garcia L</searchLink>; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France.<br /><searchLink fieldCode="AU" term="%22Blot+S%22">Blot S</searchLink>; Unité de Neurologie, Ecole Nationale Vétérinaire d'Alfort, Université Paris Est, Créteil, France.<br /><searchLink fieldCode="AU" term="%22Ritvos+O%22">Ritvos O</searchLink>; Department of Bacteriology and Immunology, Haartman Institute, University of Helsinki, Helsinki, Finland.<br /><searchLink fieldCode="AU" term="%22Bendahan+D%22">Bendahan D</searchLink>; Aix-Marseille Université, Centre National de la Recherche Scientifique, Centre de Resonance Magnetique Biologique et Medicale UMR 7339, Marseille, France.<br /><searchLink fieldCode="AU" term="%22Ferry+A%22">Ferry A</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; Université Paris Descartes, Paris, France.<br /><searchLink fieldCode="AU" term="%22Ventura-Clapier+R%22">Ventura-Clapier R</searchLink>; INSERM U 769, Université Paris-Sud, Châtenay-Malabry, France.<br /><searchLink fieldCode="AU" term="%22Schuelke+M%22">Schuelke M</searchLink>; Department of Neuropediatrics and NeuroCure Clinical Research Center, Charité Universitätsmedizin Berlin, Berlin, Germany. Electronic address: markus.schuelke@charite.de.<br /><searchLink fieldCode="AU" term="%22Amthor+H%22">Amthor H</searchLink>; Université Pierre et Marie Curie, Institut de Myologie, Unité mixte de recherche UPMC-AIM UM 76, INSERM U 974, CNRS UMR 7215, Paris, France; UFR des Sciences de la Santé, Université de Versailles Saint-Quentin-en-Yvelines, Montigny-le-Bretonneux, France; Service Génétique Médicale, CHU Necker-Enfants Malades, Université Paris Descartes, Paris, France. Electronic address: helge.amthor@uvsq.fr.
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