Nonallele specific silencing of ataxin-7 improves disease phenotypes in a mouse model of SCA7.

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Bibliographic Details
Title: Nonallele specific silencing of ataxin-7 improves disease phenotypes in a mouse model of SCA7.
Authors: Ramachandran PS; Interdisciplinary program in Genetics, University of Iowa, Iowa City, Iowa, USA., Boudreau RL; Department of Internal Medicine, University of Iowa, Iowa City, Iowa, USA., Schaefer KA; Department of Internal Medicine, University of Iowa, Iowa City, Iowa, USA., La Spada AR; Department of Pediatrics, Cellular and Molecular Medicine, and Neurosciences, Division of Biological Sciences, the Institute for Genomic Medicine, and the Sanford Consortium for Regenerative Medicine, University of California, San Diego, La Jolla, California, USA., Davidson BL; 1] Interdisciplinary program in Genetics, University of Iowa, Iowa City, Iowa, USA [2] Department of Internal Medicine, University of Iowa, Iowa City, Iowa, USA [3] Department of Neurology, University of Iowa, Iowa City, Iowa, USA [4] Department of Physiology and Biophysics, University of Iowa, Iowa City, Iowa, USA.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2014 Sep; Vol. 22 (9), pp. 1635-42. Date of Electronic Publication: 2014 Jun 16.
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1525-0024
DOI:10.1038/mt.2014.108