| Authors: |
Cortes CJ; 1] Department of Pediatrics, University of California, San Diego, La Jolla, California, USA. [2]., Miranda HC; 1] Department of Pediatrics, University of California, San Diego, La Jolla, California, USA. [2] Department of Cellular &Molecular Medicine, University of California, San Diego, La Jolla, California, USA. [3]., Frankowski H; Department of Pediatrics, University of California, San Diego, La Jolla, California, USA., Batlevi Y; Department of Pediatrics, University of California, San Diego, La Jolla, California, USA., Young JE; Department of Cellular &Molecular Medicine, University of California, San Diego, La Jolla, California, USA., Le A; Department of Pediatrics, University of California, San Diego, La Jolla, California, USA., Ivanov N; 1] Center on Human Development &Disability, University of Washington, Seattle, Washington, USA. [2] Department of Neurology, University of Washington, Seattle, Washington, USA., Sopher BL; Department of Neurology, University of Washington, Seattle, Washington, USA., Carromeu C; Department of Pediatrics, University of California, San Diego, La Jolla, California, USA., Muotri AR; 1] Department of Pediatrics, University of California, San Diego, La Jolla, California, USA. [2] Department of Cellular &Molecular Medicine, University of California, San Diego, La Jolla, California, USA. [3] Department of Neurosciences, University of California, San Diego, La Jolla, California, USA. [4] Institute for Genomic Medicine, University of California, San Diego, La Jolla, California, USA. [5] Sanford Consortium for Regenerative Medicine, University of California, San Diego, La Jolla, California, USA. [6] Rady Children's Hospital, San Diego, California, USA., Garden GA; 1] Center on Human Development &Disability, University of Washington, Seattle, Washington, USA. [2] Department of Neurology, University of Washington, Seattle, Washington, USA., La Spada AR; 1] Department of Pediatrics, University of California, San Diego, La Jolla, California, USA. [2] Department of Cellular &Molecular Medicine, University of California, San Diego, La Jolla, California, USA. [3] Department of Neurosciences, University of California, San Diego, La Jolla, California, USA. [4] Institute for Genomic Medicine, University of California, San Diego, La Jolla, California, USA. [5] Sanford Consortium for Regenerative Medicine, University of California, San Diego, La Jolla, California, USA. [6] Rady Children's Hospital, San Diego, California, USA. [7] Division of Biological Sciences, University of California, San Diego, La Jolla, California, USA. |