Long-term correction of Sandhoff disease following intravenous delivery of rAAV9 to mouse neonates.
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| Title: | Long-term correction of Sandhoff disease following intravenous delivery of rAAV9 to mouse neonates. |
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| Authors: | Walia JS; 1] Department of Pediatrics, Queen's University, Kingston, Ontario, Canada [2] Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada [3] Department of Pediatrics & Child Health, University of Manitoba, Winnipeg, Manitoba, Canada [4] Manitoba Institute of Child Health, Winnipeg, Manitoba, Canada., Altaleb N; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada., Bello A; 1] Department of Medical Microbiology, University of Manitoba, Winnipeg, Manitoba, Canada [2] Special Pathogens Program, Public Health Agency of Canada, Winnipeg, Manitoba, Canada., Kruck C; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada., LaFave MC; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA., Varshney GK; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA., Burgess SM; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA., Chowdhury B; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada., Hurlbut D; Department of Pathology & Molecular Medicine, Queen's University, Kingston, Ontario, Canada., Hemming R; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada., Kobinger GP; 1] Department of Medical Microbiology, University of Manitoba, Winnipeg, Manitoba, Canada [2] Special Pathogens Program, Public Health Agency of Canada, Winnipeg, Manitoba, Canada., Triggs-Raine B; 1] Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada [2] Department of Pediatrics & Child Health, University of Manitoba, Winnipeg, Manitoba, Canada [3] Manitoba Institute of Child Health, Winnipeg, Manitoba, Canada. |
| Source: | Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2015 Mar; Vol. 23 (3), pp. 414-22. Date of Electronic Publication: 2014 Dec 17. |
| Publication Type: | Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 25515709 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long-term correction of Sandhoff disease following intravenous delivery of rAAV9 to mouse neonates. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Walia+JS%22">Walia JS</searchLink>; 1] Department of Pediatrics, Queen's University, Kingston, Ontario, Canada [2] Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada [3] Department of Pediatrics & Child Health, University of Manitoba, Winnipeg, Manitoba, Canada [4] Manitoba Institute of Child Health, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Altaleb+N%22">Altaleb N</searchLink>; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Bello+A%22">Bello A</searchLink>; 1] Department of Medical Microbiology, University of Manitoba, Winnipeg, Manitoba, Canada [2] Special Pathogens Program, Public Health Agency of Canada, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Kruck+C%22">Kruck C</searchLink>; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22LaFave+MC%22">LaFave MC</searchLink>; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Varshney+GK%22">Varshney GK</searchLink>; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Burgess+SM%22">Burgess SM</searchLink>; Developmental Genomics Section, Translational and Functional Genomics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA.<br /><searchLink fieldCode="AU" term="%22Chowdhury+B%22">Chowdhury B</searchLink>; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Hurlbut+D%22">Hurlbut D</searchLink>; Department of Pathology & Molecular Medicine, Queen's University, Kingston, Ontario, Canada.<br /><searchLink fieldCode="AU" term="%22Hemming+R%22">Hemming R</searchLink>; Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Kobinger+GP%22">Kobinger GP</searchLink>; 1] Department of Medical Microbiology, University of Manitoba, Winnipeg, Manitoba, Canada [2] Special Pathogens Program, Public Health Agency of Canada, Winnipeg, Manitoba, Canada.<br /><searchLink fieldCode="AU" term="%22Triggs-Raine+B%22">Triggs-Raine B</searchLink>; 1] Department of Biochemistry & Medical Genetics, University of Manitoba, Winnipeg, Manitoba, Canada [2] Department of Pediatrics & Child Health, University of Manitoba, Winnipeg, Manitoba, Canada [3] Manitoba Institute of Child Health, Winnipeg, Manitoba, Canada. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22100890581%22">Molecular therapy : the journal of the American Society of Gene Therapy</searchLink> [Mol Ther] 2015 Mar; Vol. 23 (3), pp. 414-22. <i>Date of Electronic Publication: </i>2014 Dec 17. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>100890581 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1525-0024 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215250016%22">15250016 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=25515709 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/mt.2014.240 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 414 Titles: – TitleFull: Long-term correction of Sandhoff disease following intravenous delivery of rAAV9 to mouse neonates. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Walia JS – PersonEntity: Name: NameFull: Altaleb N – PersonEntity: Name: NameFull: Bello A – PersonEntity: Name: NameFull: Kruck C – PersonEntity: Name: NameFull: LaFave MC – PersonEntity: Name: NameFull: Varshney GK – PersonEntity: Name: NameFull: Burgess SM – PersonEntity: Name: NameFull: Chowdhury B – PersonEntity: Name: NameFull: Hurlbut D – PersonEntity: Name: NameFull: Hemming R – PersonEntity: Name: NameFull: Kobinger GP – PersonEntity: Name: NameFull: Triggs-Raine B IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 03 Text: 2015 Mar Type: published Y: 2015 Identifiers: – Type: issn-electronic Value: 1525-0024 Numbering: – Type: volume Value: 23 – Type: issue Value: 3 Titles: – TitleFull: Molecular therapy : the journal of the American Society of Gene Therapy Type: main |
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