Rescue of an in vitro neuron phenotype identified in Niemann-Pick disease, type C1 induced pluripotent stem cell-derived neurons by modulating the WNT pathway and calcium signaling. - Efthymiou AG; Steiner J; Pavan WJ; Wincovitch S; Larson DM; Porter FD; Rao MS; Malik N (Stem cells translational medicine, 2015)