Impact of eculizumab treatment on paroxysmal nocturnal hemoglobinuria: a treatment versus no-treatment study.

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Title: Impact of eculizumab treatment on paroxysmal nocturnal hemoglobinuria: a treatment versus no-treatment study.
Authors: Loschi M; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Hematology Department, Centre Henri BECQUEREL, Rouen, France., Porcher R; Center for Clinical Epidemiology, AP-HP, Hotel-Dieu Hospital, Inserm U1153, University Paris Descartes, Paris, France., Barraco F; Hematology Department, Centre Hospitalier Lyon Sud, Pierre Bénite, France., Terriou L; Hematology Department, Hôpital Claude Huriez, Lille, France., Mohty M; Hematology Department, AP-HP, Saint Antoine Hospital, Paris, France., de Guibert S; Hematology Department, University Hospital Pontchaillou, Rennes, France., Mahe B; Hematology Department, University Hospital, Nantes, France., Lemal R; Hematology Department, University Hospital, Clermont Ferrand, France., Dumas PY; Hematology Department, Groupe Hospitalier Sud, Pessac, France., Etienne G; Hematology Department, Groupe Hospitalier Sud, Pessac, France., Jardin F; Hematology Department, Centre Henri BECQUEREL, Rouen, France., Royer B; Hematology Department, University Hospital Amiens Sud, Amiens, France., Bordessoule D; Hematology Department, University Hospital, Limoges, France., Rohrlich PS; Hematology Department, University Hospital L'archer, Nice, France., Fornecker LM; Hematology Department, University Hospital Hautepierre, Strasbourg, France., Salanoubat C; Hematology Department, Hospital Sud Francilien, Corbeil, France., Maury S; Hematology Department, AP-HP, Henri-Mondor Hospital, Créteil, France., Cahn JY; Hematology Department, University Hospital, Grenoble, France., Vincent L; Hematology Department, University Hospital, Montpellier, France., Sene T; Internal Medicine Department, Foch Hospital, Paris, France., Rigaudeau S; Hematology Department, Versailles Hospital, Versailles, France., Nguyen S; Hematology Department, AP-HP, Pitié Salpetriere Hospital, Paris, France., Lepretre AC; Transfusion Department, Etablissement Français Du Sang, Site Saint-Louis, Paris, France., Mary JY; Statistics, AP-HP, Saint-Louis Hospital, Inserm U1153, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France., Corront B; Hematology Department, Annecy Hospital, France., Socie G; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France., Peffault de Latour R; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France.
Source: American journal of hematology [Am J Hematol] 2016 Jun; Vol. 91 (4), pp. 366-70.
Publication Type: Journal Article
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE
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  Data: <searchLink fieldCode="AU" term="%22Loschi+M%22">Loschi M</searchLink>; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Hematology Department, Centre Henri BECQUEREL, Rouen, France.<br /><searchLink fieldCode="AU" term="%22Porcher+R%22">Porcher R</searchLink>; Center for Clinical Epidemiology, AP-HP, Hotel-Dieu Hospital, Inserm U1153, University Paris Descartes, Paris, France.<br /><searchLink fieldCode="AU" term="%22Barraco+F%22">Barraco F</searchLink>; Hematology Department, Centre Hospitalier Lyon Sud, Pierre Bénite, France.<br /><searchLink fieldCode="AU" term="%22Terriou+L%22">Terriou L</searchLink>; Hematology Department, Hôpital Claude Huriez, Lille, France.<br /><searchLink fieldCode="AU" term="%22Mohty+M%22">Mohty M</searchLink>; Hematology Department, AP-HP, Saint Antoine Hospital, Paris, France.<br /><searchLink fieldCode="AU" term="%22de+Guibert+S%22">de Guibert S</searchLink>; Hematology Department, University Hospital Pontchaillou, Rennes, France.<br /><searchLink fieldCode="AU" term="%22Mahe+B%22">Mahe B</searchLink>; Hematology Department, University Hospital, Nantes, France.<br /><searchLink fieldCode="AU" term="%22Lemal+R%22">Lemal R</searchLink>; Hematology Department, University Hospital, Clermont Ferrand, France.<br /><searchLink fieldCode="AU" term="%22Dumas+PY%22">Dumas PY</searchLink>; Hematology Department, Groupe Hospitalier Sud, Pessac, France.<br /><searchLink fieldCode="AU" term="%22Etienne+G%22">Etienne G</searchLink>; Hematology Department, Groupe Hospitalier Sud, Pessac, France.<br /><searchLink fieldCode="AU" term="%22Jardin+F%22">Jardin F</searchLink>; Hematology Department, Centre Henri BECQUEREL, Rouen, France.<br /><searchLink fieldCode="AU" term="%22Royer+B%22">Royer B</searchLink>; Hematology Department, University Hospital Amiens Sud, Amiens, France.<br /><searchLink fieldCode="AU" term="%22Bordessoule+D%22">Bordessoule D</searchLink>; Hematology Department, University Hospital, Limoges, France.<br /><searchLink fieldCode="AU" term="%22Rohrlich+PS%22">Rohrlich PS</searchLink>; Hematology Department, University Hospital L'archer, Nice, France.<br /><searchLink fieldCode="AU" term="%22Fornecker+LM%22">Fornecker LM</searchLink>; Hematology Department, University Hospital Hautepierre, Strasbourg, France.<br /><searchLink fieldCode="AU" term="%22Salanoubat+C%22">Salanoubat C</searchLink>; Hematology Department, Hospital Sud Francilien, Corbeil, France.<br /><searchLink fieldCode="AU" term="%22Maury+S%22">Maury S</searchLink>; Hematology Department, AP-HP, Henri-Mondor Hospital, Créteil, France.<br /><searchLink fieldCode="AU" term="%22Cahn+JY%22">Cahn JY</searchLink>; Hematology Department, University Hospital, Grenoble, France.<br /><searchLink fieldCode="AU" term="%22Vincent+L%22">Vincent L</searchLink>; Hematology Department, University Hospital, Montpellier, France.<br /><searchLink fieldCode="AU" term="%22Sene+T%22">Sene T</searchLink>; Internal Medicine Department, Foch Hospital, Paris, France.<br /><searchLink fieldCode="AU" term="%22Rigaudeau+S%22">Rigaudeau S</searchLink>; Hematology Department, Versailles Hospital, Versailles, France.<br /><searchLink fieldCode="AU" term="%22Nguyen+S%22">Nguyen S</searchLink>; Hematology Department, AP-HP, Pitié Salpetriere Hospital, Paris, France.<br /><searchLink fieldCode="AU" term="%22Lepretre+AC%22">Lepretre AC</searchLink>; Transfusion Department, Etablissement Français Du Sang, Site Saint-Louis, Paris, France.<br /><searchLink fieldCode="AU" term="%22Mary+JY%22">Mary JY</searchLink>; Statistics, AP-HP, Saint-Louis Hospital, Inserm U1153, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France.<br /><searchLink fieldCode="AU" term="%22Corront+B%22">Corront B</searchLink>; Hematology Department, Annecy Hospital, France.<br /><searchLink fieldCode="AU" term="%22Socie+G%22">Socie G</searchLink>; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France.<br /><searchLink fieldCode="AU" term="%22Peffault+de+Latour+R%22">Peffault de Latour R</searchLink>; Hematology-Transplantation Department, AP-HP, Saint-Louis Hospital, Paris, France.; Sorbonne Paris Cité, University Paris Diderot, Paris, France.
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