In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA.
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| Title: | In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA. |
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| Authors: | Landau DJ; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA., Brooks ED; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Division of Laboratory Animal Resources, Duke University Medical Center, Durham, North Carolina, USA., Perez-Pinera P; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.; Current address: Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, Illinois, USA., Amarasekara H; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Current address: Michael E. DeBakey Department of Surgery, Division of Cardiothoracic Surgery, CHI St. Luke's Health-Baylor St. Luke's Medical Center, Houston, Texas, USA., Mefferd A; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA., Li S; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA., Bird A; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA., Gersbach CA; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA., Koeberl DD; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA. |
| Source: | Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2016 Apr; Vol. 24 (4), pp. 697-706. Date of Electronic Publication: 2016 Feb 11. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 26865405 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Landau+DJ%22">Landau DJ</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Brooks+ED%22">Brooks ED</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Division of Laboratory Animal Resources, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Perez-Pinera+P%22">Perez-Pinera P</searchLink>; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.; Current address: Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Amarasekara+H%22">Amarasekara H</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Current address: Michael E. DeBakey Department of Surgery, Division of Cardiothoracic Surgery, CHI St. Luke's Health-Baylor St. Luke's Medical Center, Houston, Texas, USA.<br /><searchLink fieldCode="AU" term="%22Mefferd+A%22">Mefferd A</searchLink>; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Li+S%22">Li S</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Bird+A%22">Bird A</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Gersbach+CA%22">Gersbach CA</searchLink>; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Koeberl+DD%22">Koeberl DD</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22100890581%22">Molecular therapy : the journal of the American Society of Gene Therapy</searchLink> [Mol Ther] 2016 Apr; Vol. 24 (4), pp. 697-706. <i>Date of Electronic Publication: </i>2016 Feb 11. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>100890581 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1525-0024 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215250016%22">15250016 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=26865405 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/mt.2016.35 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 697 Titles: – TitleFull: In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Landau DJ – PersonEntity: Name: NameFull: Brooks ED – PersonEntity: Name: NameFull: Perez-Pinera P – PersonEntity: Name: NameFull: Amarasekara H – PersonEntity: Name: NameFull: Mefferd A – PersonEntity: Name: NameFull: Li S – PersonEntity: Name: NameFull: Bird A – PersonEntity: Name: NameFull: Gersbach CA – PersonEntity: Name: NameFull: Koeberl DD IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 04 Text: 2016 Apr Type: published Y: 2016 Identifiers: – Type: issn-electronic Value: 1525-0024 Numbering: – Type: volume Value: 24 – Type: issue Value: 4 Titles: – TitleFull: Molecular therapy : the journal of the American Society of Gene Therapy Type: main |
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