In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA.

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Title: In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA.
Authors: Landau DJ; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA., Brooks ED; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Division of Laboratory Animal Resources, Duke University Medical Center, Durham, North Carolina, USA., Perez-Pinera P; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.; Current address: Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, Illinois, USA., Amarasekara H; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Current address: Michael E. DeBakey Department of Surgery, Division of Cardiothoracic Surgery, CHI St. Luke's Health-Baylor St. Luke's Medical Center, Houston, Texas, USA., Mefferd A; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA., Li S; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA., Bird A; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA., Gersbach CA; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA., Koeberl DD; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2016 Apr; Vol. 24 (4), pp. 697-706. Date of Electronic Publication: 2016 Feb 11.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA.
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  Data: <searchLink fieldCode="AU" term="%22Landau+DJ%22">Landau DJ</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Brooks+ED%22">Brooks ED</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Division of Laboratory Animal Resources, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Perez-Pinera+P%22">Perez-Pinera P</searchLink>; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.; Current address: Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Amarasekara+H%22">Amarasekara H</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Current address: Michael E. DeBakey Department of Surgery, Division of Cardiothoracic Surgery, CHI St. Luke's Health-Baylor St. Luke's Medical Center, Houston, Texas, USA.<br /><searchLink fieldCode="AU" term="%22Mefferd+A%22">Mefferd A</searchLink>; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Li+S%22">Li S</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Bird+A%22">Bird A</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Gersbach+CA%22">Gersbach CA</searchLink>; Department of Biomedical Engineering, Duke University, Durham, North Carolina, USA.<br /><searchLink fieldCode="AU" term="%22Koeberl+DD%22">Koeberl DD</searchLink>; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, North Carolina, USA.; Department of Molecular Genetics and Microbiology, Duke University, Durham, North Carolina, USA.
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  Data: <searchLink fieldCode="JN" term="%22100890581%22">Molecular therapy : the journal of the American Society of Gene Therapy</searchLink> [Mol Ther] 2016 Apr; Vol. 24 (4), pp. 697-706. <i>Date of Electronic Publication: </i>2016 Feb 11.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>100890581 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1525-0024 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215250016%22">15250016 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther <i>Subsets: </i>MEDLINE
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        Value: 10.1038/mt.2016.35
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              Text: 2016 Apr
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