Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.

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Title: Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.
Authors: Peccate C; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France., Mollard A; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France., Le Hir M; Université de Versailles St-Quentin, INSERM U1179, LIA BAHN CSM, Montigny-le-Bretonneux, France., Julien L; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France., McClorey G; Department of Physiology, Anatomy and Genetics, South Parks Road, Oxford, OX1 3QX, UK., Jarmin S; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK., Le Heron A; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK., Dickson G; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK., Benkhelifa-Ziyyat S; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France., Piétri-Rouxel F; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France., Wood MJ; Department of Physiology, Anatomy and Genetics, South Parks Road, Oxford, OX1 3QX, UK., Voit T; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.; NIHR Biomedical Research Centre, Institute of Child Health, University College London, 30 Guilford Street, London, WC1N 1EH, UK., Lorain S; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France stephanie.lorain@upmc.fr.
Source: Human molecular genetics [Hum Mol Genet] 2016 Aug 15; Vol. 25 (16), pp. 3555-3563. Date of Electronic Publication: 2016 Jul 04.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: IRL Press at Oxford University Press Country of Publication: England NLM ID: 9208958 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1460-2083 (Electronic) Linking ISSN: 09646906 NLM ISO Abbreviation: Hum Mol Genet Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1460-2083
DOI:10.1093/hmg/ddw201