Transformation in pretreatment manifestations of Gaucher disease type 1 during two decades of alglucerase/imiglucerase enzyme replacement therapy in the International Collaborative Gaucher Group (ICGG) Gaucher Registry.

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Title: Transformation in pretreatment manifestations of Gaucher disease type 1 during two decades of alglucerase/imiglucerase enzyme replacement therapy in the International Collaborative Gaucher Group (ICGG) Gaucher Registry.
Authors: Mistry PK; Department of Internal Medicine, Yale University School of Medicine, New Haven, Connecticut., Batista JL; Sanofi Genzyme, Cambridge, Massachusetts., Andersson HC; Hayward Genetics Center, Tulane University Medical School, New Orleans, Louisiana., Balwani M; Icahn School of Medicine at Mount Sinai, New York City, New York., Burrow TA; College of Medicine, University of Arkansas for Medical Sciences, Little Rock, Arkansas., Charrow J; Northwestern University Feinberg School of Medicine, Chicago, Illinois., Kaplan P; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania., Khan A; The University of Calgary, Calgary, Alberta, Canada., Kishnani PS; Division of Medical Genetics, Duke University School of Medicine, Durham, North Carolina., Kolodny EH; New York University School of Medicine, New York, New York., Rosenbloom B; Cedars-Sinai/Tower Hematology Oncology, Beverly Hills, California., Scott CR; University of Washington, Seattle, Washington., Weinreb N; Departments of Human Genetics and Medicine (Hematology), University of Miami Miller School of Medicine, Miami, Florida.
Source: American journal of hematology [Am J Hematol] 2017 Sep; Vol. 92 (9), pp. 929-939. Date of Electronic Publication: 2017 Jul 07.
Publication Type: Clinical Trial; Journal Article; Multicenter Study
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Transformation in pretreatment manifestations of Gaucher disease type 1 during two decades of alglucerase/imiglucerase enzyme replacement therapy in the International Collaborative Gaucher Group (ICGG) Gaucher Registry.
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  Data: <searchLink fieldCode="AU" term="%22Mistry+PK%22">Mistry PK</searchLink>; Department of Internal Medicine, Yale University School of Medicine, New Haven, Connecticut.<br /><searchLink fieldCode="AU" term="%22Batista+JL%22">Batista JL</searchLink>; Sanofi Genzyme, Cambridge, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Andersson+HC%22">Andersson HC</searchLink>; Hayward Genetics Center, Tulane University Medical School, New Orleans, Louisiana.<br /><searchLink fieldCode="AU" term="%22Balwani+M%22">Balwani M</searchLink>; Icahn School of Medicine at Mount Sinai, New York City, New York.<br /><searchLink fieldCode="AU" term="%22Burrow+TA%22">Burrow TA</searchLink>; College of Medicine, University of Arkansas for Medical Sciences, Little Rock, Arkansas.<br /><searchLink fieldCode="AU" term="%22Charrow+J%22">Charrow J</searchLink>; Northwestern University Feinberg School of Medicine, Chicago, Illinois.<br /><searchLink fieldCode="AU" term="%22Kaplan+P%22">Kaplan P</searchLink>; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania.<br /><searchLink fieldCode="AU" term="%22Khan+A%22">Khan A</searchLink>; The University of Calgary, Calgary, Alberta, Canada.<br /><searchLink fieldCode="AU" term="%22Kishnani+PS%22">Kishnani PS</searchLink>; Division of Medical Genetics, Duke University School of Medicine, Durham, North Carolina.<br /><searchLink fieldCode="AU" term="%22Kolodny+EH%22">Kolodny EH</searchLink>; New York University School of Medicine, New York, New York.<br /><searchLink fieldCode="AU" term="%22Rosenbloom+B%22">Rosenbloom B</searchLink>; Cedars-Sinai/Tower Hematology Oncology, Beverly Hills, California.<br /><searchLink fieldCode="AU" term="%22Scott+CR%22">Scott CR</searchLink>; University of Washington, Seattle, Washington.<br /><searchLink fieldCode="AU" term="%22Weinreb+N%22">Weinreb N</searchLink>; Departments of Human Genetics and Medicine (Hematology), University of Miami Miller School of Medicine, Miami, Florida.
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  Data: Clinical Trial; Journal Article; Multicenter Study
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