Development of gene therapies-lessons from nusinersen.
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| Title: | Development of gene therapies-lessons from nusinersen. |
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| Authors: | Xu L; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Irony I; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Bryan WW; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Dunn B; Division of Neurology Products, Office of New Drugs, Center for Drug Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA. |
| Source: | Gene therapy [Gene Ther] 2017 Sep; Vol. 24 (9), pp. 527-528. Date of Electronic Publication: 2017 Jul 24. |
| Publication Type: | Journal Article; Review |
| Journal Info: | Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 28737743 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Development of gene therapies-lessons from nusinersen. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Xu+L%22">Xu L</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Irony+I%22">Irony I</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Bryan+WW%22">Bryan WW</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Dunn+B%22">Dunn B</searchLink>; Division of Neurology Products, Office of New Drugs, Center for Drug Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%229421525%22">Gene therapy</searchLink> [Gene Ther] 2017 Sep; Vol. 24 (9), pp. 527-528. <i>Date of Electronic Publication: </i>2017 Jul 24. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Review – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Nature+Publishing+Group%22">Nature Publishing Group </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9421525 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1476-5462 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2209697128%22">09697128 </searchLink><i>NLM ISO Abbreviation: </i>Gene Ther <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=28737743 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/gt.2017.64 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 527 Titles: – TitleFull: Development of gene therapies-lessons from nusinersen. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Xu L – PersonEntity: Name: NameFull: Irony I – PersonEntity: Name: NameFull: Bryan WW – PersonEntity: Name: NameFull: Dunn B IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 09 Text: 2017 Sep Type: published Y: 2017 Identifiers: – Type: issn-electronic Value: 1476-5462 Numbering: – Type: volume Value: 24 – Type: issue Value: 9 Titles: – TitleFull: Gene therapy Type: main |
| ResultId | 1 |