Development of gene therapies-lessons from nusinersen.

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Title: Development of gene therapies-lessons from nusinersen.
Authors: Xu L; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Irony I; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Bryan WW; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA., Dunn B; Division of Neurology Products, Office of New Drugs, Center for Drug Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.
Source: Gene therapy [Gene Ther] 2017 Sep; Vol. 24 (9), pp. 527-528. Date of Electronic Publication: 2017 Jul 24.
Publication Type: Journal Article; Review
Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Xu+L%22">Xu L</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Irony+I%22">Irony I</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Bryan+WW%22">Bryan WW</searchLink>; Office of Tissues and Advanced Therapies, Center for Biologics Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.<br /><searchLink fieldCode="AU" term="%22Dunn+B%22">Dunn B</searchLink>; Division of Neurology Products, Office of New Drugs, Center for Drug Evaluation and Research, United States Food and Drug Administration, Silver Spring, MD, USA.
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  Data: <searchLink fieldCode="JN" term="%229421525%22">Gene therapy</searchLink> [Gene Ther] 2017 Sep; Vol. 24 (9), pp. 527-528. <i>Date of Electronic Publication: </i>2017 Jul 24.
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        Value: 10.1038/gt.2017.64
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        Text: English
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        StartPage: 527
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      – TitleFull: Development of gene therapies-lessons from nusinersen.
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            NameFull: Xu L
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            NameFull: Irony I
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            NameFull: Bryan WW
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            NameFull: Dunn B
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              M: 09
              Text: 2017 Sep
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              Y: 2017
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              Value: 9
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            – TitleFull: Gene therapy
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