Somatic Gene Editing of GUCY2D by AAV-CRISPR/Cas9 Alters Retinal Structure and Function in Mouse and Macaque.

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Bibliographic Details
Title: Somatic Gene Editing of GUCY2D by AAV-CRISPR/Cas9 Alters Retinal Structure and Function in Mouse and Macaque.
Authors: McCullough KT; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida., Boye SL; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida., Fajardo D; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida., Calabro K; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida., Peterson JJ; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida., Strang CE; 2 Department of Ophthalmology, University of Alabama at Birmingham, Birmingham, Alabama., Chakraborty D; 2 Department of Ophthalmology, University of Alabama at Birmingham, Birmingham, Alabama., Gloskowski S; 3 Editas Medicine, Cambridge, Massachusetts., Haskett S; 3 Editas Medicine, Cambridge, Massachusetts., Samuelsson S; 3 Editas Medicine, Cambridge, Massachusetts., Jiang H; 3 Editas Medicine, Cambridge, Massachusetts., Witherspoon CD; 2 Department of Ophthalmology, University of Alabama at Birmingham, Birmingham, Alabama., Gamlin PD; 2 Department of Ophthalmology, University of Alabama at Birmingham, Birmingham, Alabama., Maeder ML; 3 Editas Medicine, Cambridge, Massachusetts., Boye SE; 1 Department of Ophthalmology, University of Florida, Gainesville, Florida.
Source: Human gene therapy [Hum Gene Ther] 2019 May; Vol. 30 (5), pp. 571-589. Date of Electronic Publication: 2018 Dec 20.
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: M.A. Liebert Country of Publication: United States NLM ID: 9008950 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1557-7422 (Electronic) Linking ISSN: 10430342 NLM ISO Abbreviation: Hum Gene Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1557-7422
DOI:10.1089/hum.2018.193