Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO© ).

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Title: Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO© ).
Authors: Taher A; American University of Beirut Medical Center, Beirut, Lebanon., Cappellini MD; Ospedale Maggiore Policlinico IRCCS, University of Milan, Milan, Italy., Viprakasit V; Siriraj Hospital, Mahidol University, Bangkok, Thailand., Sutcharitchan P; Chulalongkorn University, Bangkok, Thailand., Mahmoud D; Celgene Corporation, Summit, New Jersey., Laadem A; Celgene Corporation, Summit, New Jersey., Khan A; Nathan S. Kline Institute for Psychiatric Research, Orangeburg, New York.; NeuroCog Trials, Durham, North Carolina., Gwaltney C; ERT, Philadelphia, Pennsylvania., Harding G; Evidera, Bethesda, Maryland., Attie K; Acceleron Pharma, Cambridge, Massachusetts., Zhang X; Acceleron Pharma, Cambridge, Massachusetts., Zou J; Celgene Corporation, Summit, New Jersey., Pariseau J; Celgene Corporation, Summit, New Jersey., Henry Hu X; Celgene Corporation, Summit, New Jersey., Kattamis A; Aghia Sophia Children's Hospital, Athens, Greece.
Source: American journal of hematology [Am J Hematol] 2019 Feb; Vol. 94 (2), pp. 177-183. Date of Electronic Publication: 2018 Nov 26.
Publication Type: Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't; Validation Study
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO<superscript>©</superscript> ).
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  Data: <searchLink fieldCode="AU" term="%22Taher+A%22">Taher A</searchLink>; American University of Beirut Medical Center, Beirut, Lebanon.<br /><searchLink fieldCode="AU" term="%22Cappellini+MD%22">Cappellini MD</searchLink>; Ospedale Maggiore Policlinico IRCCS, University of Milan, Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Viprakasit+V%22">Viprakasit V</searchLink>; Siriraj Hospital, Mahidol University, Bangkok, Thailand.<br /><searchLink fieldCode="AU" term="%22Sutcharitchan+P%22">Sutcharitchan P</searchLink>; Chulalongkorn University, Bangkok, Thailand.<br /><searchLink fieldCode="AU" term="%22Mahmoud+D%22">Mahmoud D</searchLink>; Celgene Corporation, Summit, New Jersey.<br /><searchLink fieldCode="AU" term="%22Laadem+A%22">Laadem A</searchLink>; Celgene Corporation, Summit, New Jersey.<br /><searchLink fieldCode="AU" term="%22Khan+A%22">Khan A</searchLink>; Nathan S. Kline Institute for Psychiatric Research, Orangeburg, New York.; NeuroCog Trials, Durham, North Carolina.<br /><searchLink fieldCode="AU" term="%22Gwaltney+C%22">Gwaltney C</searchLink>; ERT, Philadelphia, Pennsylvania.<br /><searchLink fieldCode="AU" term="%22Harding+G%22">Harding G</searchLink>; Evidera, Bethesda, Maryland.<br /><searchLink fieldCode="AU" term="%22Attie+K%22">Attie K</searchLink>; Acceleron Pharma, Cambridge, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Zhang+X%22">Zhang X</searchLink>; Acceleron Pharma, Cambridge, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Zou+J%22">Zou J</searchLink>; Celgene Corporation, Summit, New Jersey.<br /><searchLink fieldCode="AU" term="%22Pariseau+J%22">Pariseau J</searchLink>; Celgene Corporation, Summit, New Jersey.<br /><searchLink fieldCode="AU" term="%22Henry+Hu+X%22">Henry Hu X</searchLink>; Celgene Corporation, Summit, New Jersey.<br /><searchLink fieldCode="AU" term="%22Kattamis+A%22">Kattamis A</searchLink>; Aghia Sophia Children's Hospital, Athens, Greece.
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  Data: <searchLink fieldCode="JN" term="%227610369%22">American journal of hematology</searchLink> [Am J Hematol] 2019 Feb; Vol. 94 (2), pp. 177-183. <i>Date of Electronic Publication: </i>2018 Nov 26.
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  Data: Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't; Validation Study
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Wiley-Blackwell%22">Wiley-Blackwell </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>7610369 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1096-8652 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203618609%22">03618609 </searchLink><i>NLM ISO Abbreviation: </i>Am J Hematol <i>Subsets: </i>MEDLINE
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        Value: 10.1002/ajh.25344
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              Text: 2019 Feb
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