Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO© ).

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Bibliographic Details
Title: Validation of a patient-reported outcomes symptom measure for patients with nontransfusion-dependent thalassemia (NTDT-PRO© ).
Authors: Taher A; American University of Beirut Medical Center, Beirut, Lebanon., Cappellini MD; Ospedale Maggiore Policlinico IRCCS, University of Milan, Milan, Italy., Viprakasit V; Siriraj Hospital, Mahidol University, Bangkok, Thailand., Sutcharitchan P; Chulalongkorn University, Bangkok, Thailand., Mahmoud D; Celgene Corporation, Summit, New Jersey., Laadem A; Celgene Corporation, Summit, New Jersey., Khan A; Nathan S. Kline Institute for Psychiatric Research, Orangeburg, New York.; NeuroCog Trials, Durham, North Carolina., Gwaltney C; ERT, Philadelphia, Pennsylvania., Harding G; Evidera, Bethesda, Maryland., Attie K; Acceleron Pharma, Cambridge, Massachusetts., Zhang X; Acceleron Pharma, Cambridge, Massachusetts., Zou J; Celgene Corporation, Summit, New Jersey., Pariseau J; Celgene Corporation, Summit, New Jersey., Henry Hu X; Celgene Corporation, Summit, New Jersey., Kattamis A; Aghia Sophia Children's Hospital, Athens, Greece.
Source: American journal of hematology [Am J Hematol] 2019 Feb; Vol. 94 (2), pp. 177-183. Date of Electronic Publication: 2018 Nov 26.
Publication Type: Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't; Validation Study
Journal Info: Publisher: Wiley-Blackwell Country of Publication: United States NLM ID: 7610369 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1096-8652 (Electronic) Linking ISSN: 03618609 NLM ISO Abbreviation: Am J Hematol Subsets: MEDLINE
Database: MEDLINE Ultimate
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