Disease progression of alpha-mannosidosis and impact on patients and carers - A UK natural history survey.

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Title: Disease progression of alpha-mannosidosis and impact on patients and carers - A UK natural history survey.
Authors: Adam J; MPS Commercial, Amersham, UK., Malone R; Chiesi Limited, Manchester, UK., Lloyd S; Chiesi Limited, Manchester, UK., Lee J; Decision Resources Group, Manchester, UK., Hendriksz CJ; Steve Biko Academic Unit, Paediatrics and Child Health, University of Pretoria, Pretoria, South Africa., Ramaswami U; Lysosomal Disorders Unit, Institute of Immunity and Transplantation, Royal Free London NHS Foundation Trust, London, UK.
Source: Molecular genetics and metabolism reports [Mol Genet Metab Rep] 2019 Jun 08; Vol. 20, pp. 100480. Date of Electronic Publication: 2019 Jun 08 (Print Publication: 2019).
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Inc Country of Publication: United States NLM ID: 101624422 Publication Model: eCollection Cited Medium: Print ISSN: 2214-4269 (Print) Linking ISSN: 22144269 NLM ISO Abbreviation: Mol Genet Metab Rep Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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PubType: Academic Journal
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  Data: <searchLink fieldCode="AU" term="%22Adam+J%22">Adam J</searchLink>; MPS Commercial, Amersham, UK.<br /><searchLink fieldCode="AU" term="%22Malone+R%22">Malone R</searchLink>; Chiesi Limited, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22Lloyd+S%22">Lloyd S</searchLink>; Chiesi Limited, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22Lee+J%22">Lee J</searchLink>; Decision Resources Group, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22Hendriksz+CJ%22">Hendriksz CJ</searchLink>; Steve Biko Academic Unit, Paediatrics and Child Health, University of Pretoria, Pretoria, South Africa.<br /><searchLink fieldCode="AU" term="%22Ramaswami+U%22">Ramaswami U</searchLink>; Lysosomal Disorders Unit, Institute of Immunity and Transplantation, Royal Free London NHS Foundation Trust, London, UK.
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  Data: <searchLink fieldCode="JN" term="%22101624422%22">Molecular genetics and metabolism reports</searchLink> [Mol Genet Metab Rep] 2019 Jun 08; Vol. 20, pp. 100480. <i>Date of Electronic Publication: </i>2019 Jun 08 (<i>Print Publication: </i>2019).
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier+Inc%22">Elsevier Inc </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101624422 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2214-4269 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222144269%22">22144269 </searchLink><i>NLM ISO Abbreviation: </i>Mol Genet Metab Rep <i>Subsets: </i>PubMed not MEDLINE
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        Value: 10.1016/j.ymgmr.2019.100480
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      – Code: eng
        Text: English
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              Text: 2019 Jun 08
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