Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging.

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Title: Brain pharmacology of intrathecal antisense oligonucleotides revealed through multimodal imaging.
Authors: Mazur C; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Powers B; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Zasadny K; Invicro, LLC, Boston, Massachusetts, USA., Sullivan JM; Invicro, LLC, Boston, Massachusetts, USA.; Biogen, Cambridge, Masschusetts, USA., Dimant H; Invicro, LLC, Boston, Massachusetts, USA., Kamme F; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Hesterman J; Invicro, LLC, Boston, Massachusetts, USA., Matson J; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Oestergaard M; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Seaman M; Invicro, LLC, Boston, Massachusetts, USA., Holt RW; Invicro, LLC, Boston, Massachusetts, USA., Qutaish M; Invicro, LLC, Boston, Massachusetts, USA., Polyak I; Invicro, LLC, Boston, Massachusetts, USA., Coelho R; Invicro, LLC, Boston, Massachusetts, USA., Gottumukkala V; Invicro, LLC, Boston, Massachusetts, USA., Gaut CM; Invicro, LLC, Boston, Massachusetts, USA., Berridge M; 3D Imaging, Little Rock, Arkansas, USA., Albargothy NJ; University of Southampton, Hampshire, United Kingdom., Kelly L; University of Southampton, Hampshire, United Kingdom., Carare RO; University of Southampton, Hampshire, United Kingdom., Hoppin J; Invicro, LLC, Boston, Massachusetts, USA., Kordasiewicz H; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Swayze EE; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA., Verma A; Biogen, Cambridge, Masschusetts, USA.
Source: JCI insight [JCI Insight] 2019 Oct 17; Vol. 4 (20). Date of Electronic Publication: 2019 Oct 17.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 101676073 Publication Model: Electronic Cited Medium: Internet ISSN: 2379-3708 (Electronic) Linking ISSN: 23793708 NLM ISO Abbreviation: JCI Insight Subsets: MEDLINE
Database: MEDLINE Ultimate
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PubType: Academic Journal
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  Data: <searchLink fieldCode="AU" term="%22Mazur+C%22">Mazur C</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Powers+B%22">Powers B</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Zasadny+K%22">Zasadny K</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Sullivan+JM%22">Sullivan JM</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.; Biogen, Cambridge, Masschusetts, USA.<br /><searchLink fieldCode="AU" term="%22Dimant+H%22">Dimant H</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Kamme+F%22">Kamme F</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Hesterman+J%22">Hesterman J</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Matson+J%22">Matson J</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Oestergaard+M%22">Oestergaard M</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Seaman+M%22">Seaman M</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Holt+RW%22">Holt RW</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Qutaish+M%22">Qutaish M</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Polyak+I%22">Polyak I</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Coelho+R%22">Coelho R</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Gottumukkala+V%22">Gottumukkala V</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Gaut+CM%22">Gaut CM</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Berridge+M%22">Berridge M</searchLink>; 3D Imaging, Little Rock, Arkansas, USA.<br /><searchLink fieldCode="AU" term="%22Albargothy+NJ%22">Albargothy NJ</searchLink>; University of Southampton, Hampshire, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Kelly+L%22">Kelly L</searchLink>; University of Southampton, Hampshire, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Carare+RO%22">Carare RO</searchLink>; University of Southampton, Hampshire, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Hoppin+J%22">Hoppin J</searchLink>; Invicro, LLC, Boston, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Kordasiewicz+H%22">Kordasiewicz H</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Swayze+EE%22">Swayze EE</searchLink>; Ionis Pharmaceuticals, Inc., Carlsbad, California, USA.<br /><searchLink fieldCode="AU" term="%22Verma+A%22">Verma A</searchLink>; Biogen, Cambridge, Masschusetts, USA.
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