Orphan drug clinical development.

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Title: Orphan drug clinical development.
Authors: Blin O; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France. Electronic address: olivier.blin@ap-hm.fr., Lefebvre MN; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France., Rascol O; Services de pharmacologie clinique et neurosciences, centre d'investigation clinique CIC 1436, NS-Park/FCRIN network, NeuroToul COEN center, université de Toulouse UPS, CHU de Toulouse, INSERM, 31000 Toulouse, France., Micallef J; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France.
Source: Therapie [Therapie] 2020 Apr; Vol. 75 (2), pp. 141-147. Date of Electronic Publication: 2020 Feb 13.
Publication Type: Journal Article; Review
Journal Info: Publisher: Elsevier Masson Country of Publication: France NLM ID: 0420544 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1958-5578 (Electronic) Linking ISSN: 00405957 NLM ISO Abbreviation: Therapie Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Blin+O%22">Blin O</searchLink>; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France. Electronic address: olivier.blin@ap-hm.fr.<br /><searchLink fieldCode="AU" term="%22Lefebvre+MN%22">Lefebvre MN</searchLink>; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France.<br /><searchLink fieldCode="AU" term="%22Rascol+O%22">Rascol O</searchLink>; Services de pharmacologie clinique et neurosciences, centre d'investigation clinique CIC 1436, NS-Park/FCRIN network, NeuroToul COEN center, université de Toulouse UPS, CHU de Toulouse, INSERM, 31000 Toulouse, France.<br /><searchLink fieldCode="AU" term="%22Micallef+J%22">Micallef J</searchLink>; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France.
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  Data: <searchLink fieldCode="JN" term="%220420544%22">Therapie</searchLink> [Therapie] 2020 Apr; Vol. 75 (2), pp. 141-147. <i>Date of Electronic Publication: </i>2020 Feb 13.
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        Value: 10.1016/j.therap.2020.02.004
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        Text: English
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              Text: 2020 Apr
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