Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients.
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| Title: | Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients. |
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| Authors: | Shi X; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Aronson SJ; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Ten Bloemendaal L; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Duijst S; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Bakker RS; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., de Waart DR; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Bortolussi G; International Centre for Genetic Engineering and Biotechnology, 34149 Trieste, Italy., Collaud F; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, INSERM, Genethon, Integrare Research Unit UMR S951, 91000 Evry, France., Oude Elferink RP; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands., Muro AF; International Centre for Genetic Engineering and Biotechnology, 34149 Trieste, Italy., Mingozzi F; Genethon, 91000 Evry, France., Ronzitti G; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, INSERM, Genethon, Integrare Research Unit UMR S951, 91000 Evry, France., Bosma PJ; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands. |
| Source: | Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2020 Dec 03; Vol. 20, pp. 287-297. Date of Electronic Publication: 2020 Dec 03 (Print Publication: 2021). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 33511243 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Shi+X%22">Shi X</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Aronson+SJ%22">Aronson SJ</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Ten+Bloemendaal+L%22">Ten Bloemendaal L</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Duijst+S%22">Duijst S</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Bakker+RS%22">Bakker RS</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22de+Waart+DR%22">de Waart DR</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Bortolussi+G%22">Bortolussi G</searchLink>; International Centre for Genetic Engineering and Biotechnology, 34149 Trieste, Italy.<br /><searchLink fieldCode="AU" term="%22Collaud+F%22">Collaud F</searchLink>; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, INSERM, Genethon, Integrare Research Unit UMR S951, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Oude+Elferink+RP%22">Oude Elferink RP</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands.<br /><searchLink fieldCode="AU" term="%22Muro+AF%22">Muro AF</searchLink>; International Centre for Genetic Engineering and Biotechnology, 34149 Trieste, Italy.<br /><searchLink fieldCode="AU" term="%22Mingozzi+F%22">Mingozzi F</searchLink>; Genethon, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Ronzitti+G%22">Ronzitti G</searchLink>; Genethon, 91000 Evry, France.; Université Paris-Saclay, Université d'Evry, INSERM, Genethon, Integrare Research Unit UMR S951, 91000 Evry, France.<br /><searchLink fieldCode="AU" term="%22Bosma+PJ%22">Bosma PJ</searchLink>; Amsterdam UMC, University of Amsterdam, Tytgat Institute for Liver and Intestinal Research, AGEM, Meibergdreef 69-71, 1105 BK Amsterdam, the Netherlands. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101624857%22">Molecular therapy. Methods & clinical development</searchLink> [Mol Ther Methods Clin Dev] 2020 Dec 03; Vol. 20, pp. 287-297. <i>Date of Electronic Publication: </i>2020 Dec 03 (<i>Print Publication: </i>2021). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101624857 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2329-0501 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2223290501%22">23290501 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Methods Clin Dev <i>Subsets: </i>PubMed not MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=33511243 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.omtm.2020.11.016 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 287 Titles: – TitleFull: Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Shi X – PersonEntity: Name: NameFull: Aronson SJ – PersonEntity: Name: NameFull: Ten Bloemendaal L – PersonEntity: Name: NameFull: Duijst S – PersonEntity: Name: NameFull: Bakker RS – PersonEntity: Name: NameFull: de Waart DR – PersonEntity: Name: NameFull: Bortolussi G – PersonEntity: Name: NameFull: Collaud F – PersonEntity: Name: NameFull: Oude Elferink RP – PersonEntity: Name: NameFull: Muro AF – PersonEntity: Name: NameFull: Mingozzi F – PersonEntity: Name: NameFull: Ronzitti G – PersonEntity: Name: NameFull: Bosma PJ IsPartOfRelationships: – BibEntity: Dates: – D: 03 M: 12 Text: 2020 Dec 03 Type: published Y: 2020 Identifiers: – Type: issn-print Value: 2329-0501 Numbering: – Type: volume Value: 20 Titles: – TitleFull: Molecular therapy. Methods & clinical development Type: main |
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