Patient and family experience with transthyretin amyloid cardiomyopathy (ATTR-CM) and polyneuropathy (ATTR-PN) amyloidosis: results of two focus groups.
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| Title: | Patient and family experience with transthyretin amyloid cardiomyopathy (ATTR-CM) and polyneuropathy (ATTR-PN) amyloidosis: results of two focus groups. |
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| Authors: | Rintell D; BridgeBio, Palo Alto, CA, USA. dr@bridgebio.com., Heath D; Amyloidosis Research Consortium, Newton, MA, USA., Braga Mendendez F; Alianza Argentina de Pacientes, Buenos Aires, Argentina., Cross E; Cross Associates, Woodland Park, NJ, USA., Cross T; Cross Associates, Woodland Park, NJ, USA., Knobel V; Eidos Therapeutics, San Francisco, CA, USA., Gagnon B; Eidos Therapeutics, San Francisco, CA, USA., Turtle C; Eidos Therapeutics, San Francisco, CA, USA., Cohen A; Eidos Therapeutics, San Francisco, CA, USA., Kalmykov E; Eidos Therapeutics, San Francisco, CA, USA., Fox J; Eidos Therapeutics, San Francisco, CA, USA. |
| Source: | Orphanet journal of rare diseases [Orphanet J Rare Dis] 2021 Feb 08; Vol. 16 (1), pp. 70. Date of Electronic Publication: 2021 Feb 08. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172 (Electronic) Linking ISSN: 17501172 NLM ISO Abbreviation: Orphanet J Rare Dis Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1750-1172 |
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| DOI: | 10.1186/s13023-021-01706-7 |