Patient and family experience with transthyretin amyloid cardiomyopathy (ATTR-CM) and polyneuropathy (ATTR-PN) amyloidosis: results of two focus groups.

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Title: Patient and family experience with transthyretin amyloid cardiomyopathy (ATTR-CM) and polyneuropathy (ATTR-PN) amyloidosis: results of two focus groups.
Authors: Rintell D; BridgeBio, Palo Alto, CA, USA. dr@bridgebio.com., Heath D; Amyloidosis Research Consortium, Newton, MA, USA., Braga Mendendez F; Alianza Argentina de Pacientes, Buenos Aires, Argentina., Cross E; Cross Associates, Woodland Park, NJ, USA., Cross T; Cross Associates, Woodland Park, NJ, USA., Knobel V; Eidos Therapeutics, San Francisco, CA, USA., Gagnon B; Eidos Therapeutics, San Francisco, CA, USA., Turtle C; Eidos Therapeutics, San Francisco, CA, USA., Cohen A; Eidos Therapeutics, San Francisco, CA, USA., Kalmykov E; Eidos Therapeutics, San Francisco, CA, USA., Fox J; Eidos Therapeutics, San Francisco, CA, USA.
Source: Orphanet journal of rare diseases [Orphanet J Rare Dis] 2021 Feb 08; Vol. 16 (1), pp. 70. Date of Electronic Publication: 2021 Feb 08.
Publication Type: Journal Article
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101266602 Publication Model: Electronic Cited Medium: Internet ISSN: 1750-1172 (Electronic) Linking ISSN: 17501172 NLM ISO Abbreviation: Orphanet J Rare Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1750-1172
DOI:10.1186/s13023-021-01706-7