Cardiac responses in paediatric Pompe disease in the ADVANCE patient cohort.

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Title: Cardiac responses in paediatric Pompe disease in the ADVANCE patient cohort.
Authors: Byrne BJ; Department of Pediatrics, College of Medicine, Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA., Colan SD; Department of Cardiology, Boston Children's Hospital, Boston, MA, USA., Kishnani PS; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA., Foster MC; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA., Sparks SE; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA., Gibson JB; Department of Clinical and Metabolic Genetics, Clinical and Metabolic Genetics, Dell Children's Medical Group, Austin, TX, USA., An Haack K; Rare Diseases, Sanofi Genzyme, Shanghai, China., Stockton DW; Department of Pediatrics, Division of Genetic, Genomic, and Metabolic Disorders, Central Michigan University, Children's Hospital of Michigan, Detroit, MI, USA., Peña LDM; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.; Department of Pediatrics, Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.; Department of Pediatrics, University of Cincinnati, College of Medicine, Cincinnati, OH, USA., Hahn SH; Departments of Pediatrics and Medicine, Biochemical Genetics Program, Seattle Children's Hospital, University of Washington, Seattle, WA, USA., Johnson J; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA., Tanpaiboon PX; Department of Genetics, Children's National Hospital, Washington, DC, USA., Leslie ND; Department of Pediatrics, Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA., Kronn D; Departments of Pathology and Pediatrics, New York Medical College, Valhalla, NY, USA., Hillman RE; Department of Pediatrics, University of Missouri Child Health, Columbia, MO, USA., Wang RY; Department of Pediatrics, Foundation of Caring Multidisciplinary Lysosomal Storage Disease Program, Children's Hospital of Orange County, Orange, CA, USA.; Department of Pediatrics, University of California, Irvine School of Medicine, Orange, CA, USA.
Corporate Authors: Pompe ADVANCE Study Consortium
Source: Cardiology in the young [Cardiol Young] 2022 Mar; Vol. 32 (3), pp. 364-373. Date of Electronic Publication: 2021 Aug 23.
Publication Type: Clinical Trial; Journal Article
Journal Info: Publisher: Cambridge University Press Country of Publication: England NLM ID: 9200019 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1467-1107 (Electronic) Linking ISSN: 10479511 NLM ISO Abbreviation: Cardiol Young Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Cardiac responses in paediatric Pompe disease in the ADVANCE patient cohort.
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  Data: <searchLink fieldCode="AU" term="%22Byrne+BJ%22">Byrne BJ</searchLink>; Department of Pediatrics, College of Medicine, Powell Gene Therapy Center, University of Florida, Gainesville, FL, USA.<br /><searchLink fieldCode="AU" term="%22Colan+SD%22">Colan SD</searchLink>; Department of Cardiology, Boston Children's Hospital, Boston, MA, USA.<br /><searchLink fieldCode="AU" term="%22Kishnani+PS%22">Kishnani PS</searchLink>; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.<br /><searchLink fieldCode="AU" term="%22Foster+MC%22">Foster MC</searchLink>; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Sparks+SE%22">Sparks SE</searchLink>; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Gibson+JB%22">Gibson JB</searchLink>; Department of Clinical and Metabolic Genetics, Clinical and Metabolic Genetics, Dell Children's Medical Group, Austin, TX, USA.<br /><searchLink fieldCode="AU" term="%22An+Haack+K%22">An Haack K</searchLink>; Rare Diseases, Sanofi Genzyme, Shanghai, China.<br /><searchLink fieldCode="AU" term="%22Stockton+DW%22">Stockton DW</searchLink>; Department of Pediatrics, Division of Genetic, Genomic, and Metabolic Disorders, Central Michigan University, Children's Hospital of Michigan, Detroit, MI, USA.<br /><searchLink fieldCode="AU" term="%22Peña+LDM%22">Peña LDM</searchLink>; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.; Department of Pediatrics, Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.; Department of Pediatrics, University of Cincinnati, College of Medicine, Cincinnati, OH, USA.<br /><searchLink fieldCode="AU" term="%22Hahn+SH%22">Hahn SH</searchLink>; Departments of Pediatrics and Medicine, Biochemical Genetics Program, Seattle Children's Hospital, University of Washington, Seattle, WA, USA.<br /><searchLink fieldCode="AU" term="%22Johnson+J%22">Johnson J</searchLink>; Biostatistics, Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Tanpaiboon+PX%22">Tanpaiboon PX</searchLink>; Department of Genetics, Children's National Hospital, Washington, DC, USA.<br /><searchLink fieldCode="AU" term="%22Leslie+ND%22">Leslie ND</searchLink>; Department of Pediatrics, Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.<br /><searchLink fieldCode="AU" term="%22Kronn+D%22">Kronn D</searchLink>; Departments of Pathology and Pediatrics, New York Medical College, Valhalla, NY, USA.<br /><searchLink fieldCode="AU" term="%22Hillman+RE%22">Hillman RE</searchLink>; Department of Pediatrics, University of Missouri Child Health, Columbia, MO, USA.<br /><searchLink fieldCode="AU" term="%22Wang+RY%22">Wang RY</searchLink>; Department of Pediatrics, Foundation of Caring Multidisciplinary Lysosomal Storage Disease Program, Children's Hospital of Orange County, Orange, CA, USA.; Department of Pediatrics, University of California, Irvine School of Medicine, Orange, CA, USA.
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  Data: <searchLink fieldCode="CA" term="%22Pompe+ADVANCE+Study+Consortium%22">Pompe ADVANCE Study Consortium</searchLink>
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  Data: <searchLink fieldCode="JN" term="%229200019%22">Cardiology in the young</searchLink> [Cardiol Young] 2022 Mar; Vol. 32 (3), pp. 364-373. <i>Date of Electronic Publication: </i>2021 Aug 23.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cambridge+University+Press%22">Cambridge University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9200019 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1467-1107 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2210479511%22">10479511 </searchLink><i>NLM ISO Abbreviation: </i>Cardiol Young <i>Subsets: </i>MEDLINE
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              Text: 2022 Mar
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