Donor source and post-transplantation cyclophosphamide influence outcome in allogeneic stem cell transplantation for GATA2 deficiency.

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Title: Donor source and post-transplantation cyclophosphamide influence outcome in allogeneic stem cell transplantation for GATA2 deficiency.
Authors: Nichols-Vinueza DX; Laboratory of Allergic Diseases, National Institute of Allergy and Infectious Diseases, National Institute of Health, Bethesda, MD, USA., Parta M; Clinical Research Directorate, Frederick National Laboratory for Cancer Research, Frederick, MD, USA., Shah NN; Pediatric Oncology Branch, National Cancer Institute, Bethesda, MD, USA., Cuellar-Rodriguez JM; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institute of Health, Bethesda, MD, USA., Bauer TR Jr; Immune Deficiency - Cellular Therapy Program, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA., West RR; Immune Deficiency - Cellular Therapy Program, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA., Hsu AP; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institute of Health, Bethesda, MD, USA., Calvo KR; Department of Laboratory Medicine, NIH Clinical Center, Bethesda, MD, USA., Steinberg SM; Biostatistics and Data Management Section, Office of the Clinical Director, Center for Cancer Research, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA., Notarangelo LD; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institute of Health, Bethesda, MD, USA., Holland SM; Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, National Institute of Health, Bethesda, MD, USA., Hickstein DD; Immune Deficiency - Cellular Therapy Program, National Cancer Institute, National Institutes of Health, Bethesda, MD, USA.
Source: British journal of haematology [Br J Haematol] 2022 Jan; Vol. 196 (1), pp. 169-178. Date of Electronic Publication: 2021 Sep 27.
Publication Type: Journal Article; Research Support, N.I.H., Intramural
Journal Info: Publisher: Wiley-Blackwell Country of Publication: England NLM ID: 0372544 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2141 (Electronic) Linking ISSN: 00071048 NLM ISO Abbreviation: Br J Haematol Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1365-2141
DOI:10.1111/bjh.17840