Muscle-directed gene therapy corrects Pompe disease and uncovers species-specific GAA immunogenicity. - Eggers M; Vannoy CH; Huang J; Purushothaman P; Brassard J; Fonck C; Meng H; Prom MJ; Lawlor MW; Cunningham J; Sadhu C; Mavilio F (EMBO molecular medicine, 2022)