Infigratinib in children with achondroplasia: the PROPEL and PROPEL 2 studies.

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Title: Infigratinib in children with achondroplasia: the PROPEL and PROPEL 2 studies.
Authors: Savarirayan R; Murdoch Children's Research Institute, Parkville, VIC 3052, Australia., De Bergua JM; Unidad de Cirugía Artroscópica (UCA), Hospital Vithas Vitoria, Vitoria-Gasteiz, Spain., Arundel P; Sheffield Children's NHS Foundation Trust, Sheffield, UK., McDevitt H; NHS Greater Glasgow and Clyde, Glasgow, UK., Cormier-Daire V; Imagine Institute, Hôpital Necker-Enfants Malades, University of Paris, Paris, France., Saraff V; Birmingham Women's and Children's NHS Foundation Trust, Birmingham, UK., Skae M; Manchester University NHS Foundation Trust, The University of Manchester, Manchester, UK., Delgado B; Campus de Teatinos sin número, Malaga, Spain., Leiva-Gea A; Instituto de Investigación Biomédica de Málaga (IBIMA), Malaga, Spain., Santos-Simarro F; Instituto de Genética Médica y Molecular (INGEMM), Unidad Multidisciplinar de Displasias Esqueléticas (UMDE), Hospital Universitario La Paz, Instituto de Investigación del Hospital Universitario La Paz (IdiPAZ), Centro de Investigación Biomédica en Red de enfermedades raras (CIBERER), Instituto de Salud Carlos III (ISCIII), Madrid, Spain., Salles JP; Hôpital des Enfants, Toulouse, France., Nicolino M; Hôpital Femme Mère Enfant, Hospices Civils de Lyon, France., Rossi M; Lyon University Hospital, Bron, France., Kannu P; Stollery Children's Hospital, University of Alberta, Edmonton, AB, Canada., Bober MB; Nemours Children's Hospital, Wilmington, DE, USA., Phillips J 3rd; Vanderbilt University Medical Center, Nashville, TN, USA., Saal H; Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA., Harmatz P; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA., Burren C; University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, UK., Gotway G; Children's Medical Center Dallas, Texas, TX, USA., Cho T; QED Therapeutics Inc., San Francisco, CA, USA., Muslimova E; QED Therapeutics Inc., San Francisco, CA, USA., Weng R; QED Therapeutics Inc., San Francisco, CA, USA., Rogoff D; QED Therapeutics Inc., San Francisco, CA, USA., Hoover-Fong J; School of Medicine, Johns Hopkins University, Baltimore, MA, USA., Irving M; Guy's and Saint Thomas' NHS Foundation Trust, London, UK.
Source: Therapeutic advances in musculoskeletal disease [Ther Adv Musculoskelet Dis] 2022 Mar 21; Vol. 14, pp. 1759720X221084848. Date of Electronic Publication: 2022 Mar 21 (Print Publication: 2022).
Publication Type: Journal Article
Journal Info: Publisher: Sage Country of Publication: England NLM ID: 101517322 Publication Model: eCollection Cited Medium: Print ISSN: 1759-720X (Print) Linking ISSN: 1759720X NLM ISO Abbreviation: Ther Adv Musculoskelet Dis Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Infigratinib in children with achondroplasia: the PROPEL and PROPEL 2 studies.
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  Data: <searchLink fieldCode="AU" term="%22Savarirayan+R%22">Savarirayan R</searchLink>; Murdoch Children's Research Institute, Parkville, VIC 3052, Australia.<br /><searchLink fieldCode="AU" term="%22De+Bergua+JM%22">De Bergua JM</searchLink>; Unidad de Cirugía Artroscópica (UCA), Hospital Vithas Vitoria, Vitoria-Gasteiz, Spain.<br /><searchLink fieldCode="AU" term="%22Arundel+P%22">Arundel P</searchLink>; Sheffield Children's NHS Foundation Trust, Sheffield, UK.<br /><searchLink fieldCode="AU" term="%22McDevitt+H%22">McDevitt H</searchLink>; NHS Greater Glasgow and Clyde, Glasgow, UK.<br /><searchLink fieldCode="AU" term="%22Cormier-Daire+V%22">Cormier-Daire V</searchLink>; Imagine Institute, Hôpital Necker-Enfants Malades, University of Paris, Paris, France.<br /><searchLink fieldCode="AU" term="%22Saraff+V%22">Saraff V</searchLink>; Birmingham Women's and Children's NHS Foundation Trust, Birmingham, UK.<br /><searchLink fieldCode="AU" term="%22Skae+M%22">Skae M</searchLink>; Manchester University NHS Foundation Trust, The University of Manchester, Manchester, UK.<br /><searchLink fieldCode="AU" term="%22Delgado+B%22">Delgado B</searchLink>; Campus de Teatinos sin número, Malaga, Spain.<br /><searchLink fieldCode="AU" term="%22Leiva-Gea+A%22">Leiva-Gea A</searchLink>; Instituto de Investigación Biomédica de Málaga (IBIMA), Malaga, Spain.<br /><searchLink fieldCode="AU" term="%22Santos-Simarro+F%22">Santos-Simarro F</searchLink>; Instituto de Genética Médica y Molecular (INGEMM), Unidad Multidisciplinar de Displasias Esqueléticas (UMDE), Hospital Universitario La Paz, Instituto de Investigación del Hospital Universitario La Paz (IdiPAZ), Centro de Investigación Biomédica en Red de enfermedades raras (CIBERER), Instituto de Salud Carlos III (ISCIII), Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Salles+JP%22">Salles JP</searchLink>; Hôpital des Enfants, Toulouse, France.<br /><searchLink fieldCode="AU" term="%22Nicolino+M%22">Nicolino M</searchLink>; Hôpital Femme Mère Enfant, Hospices Civils de Lyon, France.<br /><searchLink fieldCode="AU" term="%22Rossi+M%22">Rossi M</searchLink>; Lyon University Hospital, Bron, France.<br /><searchLink fieldCode="AU" term="%22Kannu+P%22">Kannu P</searchLink>; Stollery Children's Hospital, University of Alberta, Edmonton, AB, Canada.<br /><searchLink fieldCode="AU" term="%22Bober+MB%22">Bober MB</searchLink>; Nemours Children's Hospital, Wilmington, DE, USA.<br /><searchLink fieldCode="AU" term="%22Phillips+J+3rd%22">Phillips J 3rd</searchLink>; Vanderbilt University Medical Center, Nashville, TN, USA.<br /><searchLink fieldCode="AU" term="%22Saal+H%22">Saal H</searchLink>; Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.<br /><searchLink fieldCode="AU" term="%22Harmatz+P%22">Harmatz P</searchLink>; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA.<br /><searchLink fieldCode="AU" term="%22Burren+C%22">Burren C</searchLink>; University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, UK.<br /><searchLink fieldCode="AU" term="%22Gotway+G%22">Gotway G</searchLink>; Children's Medical Center Dallas, Texas, TX, USA.<br /><searchLink fieldCode="AU" term="%22Cho+T%22">Cho T</searchLink>; QED Therapeutics Inc., San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Muslimova+E%22">Muslimova E</searchLink>; QED Therapeutics Inc., San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Weng+R%22">Weng R</searchLink>; QED Therapeutics Inc., San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Rogoff+D%22">Rogoff D</searchLink>; QED Therapeutics Inc., San Francisco, CA, USA.<br /><searchLink fieldCode="AU" term="%22Hoover-Fong+J%22">Hoover-Fong J</searchLink>; School of Medicine, Johns Hopkins University, Baltimore, MA, USA.<br /><searchLink fieldCode="AU" term="%22Irving+M%22">Irving M</searchLink>; Guy's and Saint Thomas' NHS Foundation Trust, London, UK.
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  Data: <searchLink fieldCode="JN" term="%22101517322%22">Therapeutic advances in musculoskeletal disease</searchLink> [Ther Adv Musculoskelet Dis] 2022 Mar 21; Vol. 14, pp. 1759720X221084848. <i>Date of Electronic Publication: </i>2022 Mar 21 (<i>Print Publication: </i>2022).
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Sage%22">Sage </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101517322 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>1759-720X (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%221759720X%22">1759720X </searchLink><i>NLM ISO Abbreviation: </i>Ther Adv Musculoskelet Dis <i>Subsets: </i>PubMed not MEDLINE
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