Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.

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Title: Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.
Authors: Estepp JH; St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Kalpatthi R; UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA., Woods G; Children's Mercy Hospital, Kansas City, Missouri, USA., Trompeter S; University College London Hospitals NHS Foundation Trust, London, UK., Liem RI; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA., Sims K; St. Jude Affiliate Clinic Baton Rouge, Baton Rouge, Los Angeles, USA., Inati A; School of Medicine, Byblos and Nini Hospital, Lebanese American University, Tripoli, Lebanon., Inusa BPD; Guy's and Saint Thomas' NHS Foundation Trust, London, UK., Campbell A; Division of Hematology, Children's National Hospital, Washington, District of Columbia, USA., Piccone C; Department of Pediatric Hematology, Carle Foundation Hospital, Urbana, Illinois, USA., Abboud MR; American University of Beirut Medical Center, Beirut, Lebanon., Smith-Whitley K; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Dixon S; Global Blood Therapeutics, South San Francisco, California, USA., Tonda M; Global Blood Therapeutics, South San Francisco, California, USA., Washington C; Global Blood Therapeutics, South San Francisco, California, USA., Griffin NM; Global Blood Therapeutics, South San Francisco, California, USA., Brown C; Emory + Children's Pediatric Institute, Atlanta, Georgia, USA.
Source: Pediatric blood & cancer [Pediatr Blood Cancer] 2022 Aug; Vol. 69 (8), pp. e29716. Date of Electronic Publication: 2022 Apr 21.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: John Wiley Country of Publication: United States NLM ID: 101186624 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1545-5017 (Electronic) Linking ISSN: 15455009 NLM ISO Abbreviation: Pediatr Blood Cancer Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1545-5017
DOI:10.1002/pbc.29716