Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.
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| Title: | Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years. |
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| Authors: | Estepp JH; St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Kalpatthi R; UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA., Woods G; Children's Mercy Hospital, Kansas City, Missouri, USA., Trompeter S; University College London Hospitals NHS Foundation Trust, London, UK., Liem RI; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA., Sims K; St. Jude Affiliate Clinic Baton Rouge, Baton Rouge, Los Angeles, USA., Inati A; School of Medicine, Byblos and Nini Hospital, Lebanese American University, Tripoli, Lebanon., Inusa BPD; Guy's and Saint Thomas' NHS Foundation Trust, London, UK., Campbell A; Division of Hematology, Children's National Hospital, Washington, District of Columbia, USA., Piccone C; Department of Pediatric Hematology, Carle Foundation Hospital, Urbana, Illinois, USA., Abboud MR; American University of Beirut Medical Center, Beirut, Lebanon., Smith-Whitley K; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Dixon S; Global Blood Therapeutics, South San Francisco, California, USA., Tonda M; Global Blood Therapeutics, South San Francisco, California, USA., Washington C; Global Blood Therapeutics, South San Francisco, California, USA., Griffin NM; Global Blood Therapeutics, South San Francisco, California, USA., Brown C; Emory + Children's Pediatric Institute, Atlanta, Georgia, USA. |
| Source: | Pediatric blood & cancer [Pediatr Blood Cancer] 2022 Aug; Vol. 69 (8), pp. e29716. Date of Electronic Publication: 2022 Apr 21. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: John Wiley Country of Publication: United States NLM ID: 101186624 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1545-5017 (Electronic) Linking ISSN: 15455009 NLM ISO Abbreviation: Pediatr Blood Cancer Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 35451176 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Estepp+JH%22">Estepp JH</searchLink>; St. Jude Children's Research Hospital, Memphis, Tennessee, USA.<br /><searchLink fieldCode="AU" term="%22Kalpatthi+R%22">Kalpatthi R</searchLink>; UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Woods+G%22">Woods G</searchLink>; Children's Mercy Hospital, Kansas City, Missouri, USA.<br /><searchLink fieldCode="AU" term="%22Trompeter+S%22">Trompeter S</searchLink>; University College London Hospitals NHS Foundation Trust, London, UK.<br /><searchLink fieldCode="AU" term="%22Liem+RI%22">Liem RI</searchLink>; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Sims+K%22">Sims K</searchLink>; St. Jude Affiliate Clinic Baton Rouge, Baton Rouge, Los Angeles, USA.<br /><searchLink fieldCode="AU" term="%22Inati+A%22">Inati A</searchLink>; School of Medicine, Byblos and Nini Hospital, Lebanese American University, Tripoli, Lebanon.<br /><searchLink fieldCode="AU" term="%22Inusa+BPD%22">Inusa BPD</searchLink>; Guy's and Saint Thomas' NHS Foundation Trust, London, UK.<br /><searchLink fieldCode="AU" term="%22Campbell+A%22">Campbell A</searchLink>; Division of Hematology, Children's National Hospital, Washington, District of Columbia, USA.<br /><searchLink fieldCode="AU" term="%22Piccone+C%22">Piccone C</searchLink>; Department of Pediatric Hematology, Carle Foundation Hospital, Urbana, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Abboud+MR%22">Abboud MR</searchLink>; American University of Beirut Medical Center, Beirut, Lebanon.<br /><searchLink fieldCode="AU" term="%22Smith-Whitley+K%22">Smith-Whitley K</searchLink>; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Dixon+S%22">Dixon S</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Tonda+M%22">Tonda M</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Washington+C%22">Washington C</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Griffin+NM%22">Griffin NM</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Brown+C%22">Brown C</searchLink>; Emory + Children's Pediatric Institute, Atlanta, Georgia, USA. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101186624%22">Pediatric blood & cancer</searchLink> [Pediatr Blood Cancer] 2022 Aug; Vol. 69 (8), pp. e29716. <i>Date of Electronic Publication: </i>2022 Apr 21. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22John+Wiley%22">John Wiley </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101186624 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1545-5017 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215455009%22">15455009 </searchLink><i>NLM ISO Abbreviation: </i>Pediatr Blood Cancer <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=35451176 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1002/pbc.29716 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: e29716 Titles: – TitleFull: Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Estepp JH – PersonEntity: Name: NameFull: Kalpatthi R – PersonEntity: Name: NameFull: Woods G – PersonEntity: Name: NameFull: Trompeter S – PersonEntity: Name: NameFull: Liem RI – PersonEntity: Name: NameFull: Sims K – PersonEntity: Name: NameFull: Inati A – PersonEntity: Name: NameFull: Inusa BPD – PersonEntity: Name: NameFull: Campbell A – PersonEntity: Name: NameFull: Piccone C – PersonEntity: Name: NameFull: Abboud MR – PersonEntity: Name: NameFull: Smith-Whitley K – PersonEntity: Name: NameFull: Dixon S – PersonEntity: Name: NameFull: Tonda M – PersonEntity: Name: NameFull: Washington C – PersonEntity: Name: NameFull: Griffin NM – PersonEntity: Name: NameFull: Brown C IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 08 Text: 2022 Aug Type: published Y: 2022 Identifiers: – Type: issn-electronic Value: 1545-5017 Numbering: – Type: volume Value: 69 – Type: issue Value: 8 Titles: – TitleFull: Pediatric blood & cancer Type: main |
| ResultId | 1 |