Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.

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Title: Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.
Authors: Estepp JH; St. Jude Children's Research Hospital, Memphis, Tennessee, USA., Kalpatthi R; UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA., Woods G; Children's Mercy Hospital, Kansas City, Missouri, USA., Trompeter S; University College London Hospitals NHS Foundation Trust, London, UK., Liem RI; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA., Sims K; St. Jude Affiliate Clinic Baton Rouge, Baton Rouge, Los Angeles, USA., Inati A; School of Medicine, Byblos and Nini Hospital, Lebanese American University, Tripoli, Lebanon., Inusa BPD; Guy's and Saint Thomas' NHS Foundation Trust, London, UK., Campbell A; Division of Hematology, Children's National Hospital, Washington, District of Columbia, USA., Piccone C; Department of Pediatric Hematology, Carle Foundation Hospital, Urbana, Illinois, USA., Abboud MR; American University of Beirut Medical Center, Beirut, Lebanon., Smith-Whitley K; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA., Dixon S; Global Blood Therapeutics, South San Francisco, California, USA., Tonda M; Global Blood Therapeutics, South San Francisco, California, USA., Washington C; Global Blood Therapeutics, South San Francisco, California, USA., Griffin NM; Global Blood Therapeutics, South San Francisco, California, USA., Brown C; Emory + Children's Pediatric Institute, Atlanta, Georgia, USA.
Source: Pediatric blood & cancer [Pediatr Blood Cancer] 2022 Aug; Vol. 69 (8), pp. e29716. Date of Electronic Publication: 2022 Apr 21.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: John Wiley Country of Publication: United States NLM ID: 101186624 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1545-5017 (Electronic) Linking ISSN: 15455009 NLM ISO Abbreviation: Pediatr Blood Cancer Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Safety and efficacy of voxelotor in pediatric patients with sickle cell disease aged 4 to 11 years.
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  Data: <searchLink fieldCode="AU" term="%22Estepp+JH%22">Estepp JH</searchLink>; St. Jude Children's Research Hospital, Memphis, Tennessee, USA.<br /><searchLink fieldCode="AU" term="%22Kalpatthi+R%22">Kalpatthi R</searchLink>; UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Woods+G%22">Woods G</searchLink>; Children's Mercy Hospital, Kansas City, Missouri, USA.<br /><searchLink fieldCode="AU" term="%22Trompeter+S%22">Trompeter S</searchLink>; University College London Hospitals NHS Foundation Trust, London, UK.<br /><searchLink fieldCode="AU" term="%22Liem+RI%22">Liem RI</searchLink>; Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Sims+K%22">Sims K</searchLink>; St. Jude Affiliate Clinic Baton Rouge, Baton Rouge, Los Angeles, USA.<br /><searchLink fieldCode="AU" term="%22Inati+A%22">Inati A</searchLink>; School of Medicine, Byblos and Nini Hospital, Lebanese American University, Tripoli, Lebanon.<br /><searchLink fieldCode="AU" term="%22Inusa+BPD%22">Inusa BPD</searchLink>; Guy's and Saint Thomas' NHS Foundation Trust, London, UK.<br /><searchLink fieldCode="AU" term="%22Campbell+A%22">Campbell A</searchLink>; Division of Hematology, Children's National Hospital, Washington, District of Columbia, USA.<br /><searchLink fieldCode="AU" term="%22Piccone+C%22">Piccone C</searchLink>; Department of Pediatric Hematology, Carle Foundation Hospital, Urbana, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Abboud+MR%22">Abboud MR</searchLink>; American University of Beirut Medical Center, Beirut, Lebanon.<br /><searchLink fieldCode="AU" term="%22Smith-Whitley+K%22">Smith-Whitley K</searchLink>; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, USA.<br /><searchLink fieldCode="AU" term="%22Dixon+S%22">Dixon S</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Tonda+M%22">Tonda M</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Washington+C%22">Washington C</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Griffin+NM%22">Griffin NM</searchLink>; Global Blood Therapeutics, South San Francisco, California, USA.<br /><searchLink fieldCode="AU" term="%22Brown+C%22">Brown C</searchLink>; Emory + Children's Pediatric Institute, Atlanta, Georgia, USA.
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  Data: <searchLink fieldCode="JN" term="%22101186624%22">Pediatric blood & cancer</searchLink> [Pediatr Blood Cancer] 2022 Aug; Vol. 69 (8), pp. e29716. <i>Date of Electronic Publication: </i>2022 Apr 21.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22John+Wiley%22">John Wiley </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101186624 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1545-5017 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215455009%22">15455009 </searchLink><i>NLM ISO Abbreviation: </i>Pediatr Blood Cancer <i>Subsets: </i>MEDLINE
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              Text: 2022 Aug
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