Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia.

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Title: Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia.
Authors: Ward LM; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario K1H 8L1, Canada., Glorieux FH; Shriners Hospitals for Children, Canada, McGill University, Montreal, Quebec H4A OA9, Canada., Whyte MP; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110,USA., Munns CF; Child Health Research Centre, The University of Queensland, Brisbane, Queensland 4072, Australia.; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia., Portale AA; Department of Pediatrics, University of California, San Francisco, San Francisco, California 94143, USA., Högler W; Department of Pediatrics and Adolescent Medicine, Johannes Kepler University Linz, Linz 4040, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Birmingham, B15 2TT, UK., Simmons JH; Department of Pediatrics, Division of Endocrinology and Diabetes, Vanderbilt University School of Medicine, Vanderbilt University, 680-8570 Nashville, Tennessee, 63110, USA., Gottesman GS; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110, USA., Padidela R; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester M13 9WL, UK., Namba N; Department of Pediatrics, Osaka Hospital, Japan.; Community Healthcare Organization.; Osaka University Graduate School of Medicine, Osaka 553-0003, Japan.; Division of Pediatrics and Perinatology, Tottori University Faculty of Medicine, Yonago, Japan., Cheong HI; Department of Pediatrics, Seoul National University Children's Hospital, Seoul 14068, South Korea., Nilsson O; Division of Pediatric Endocrinology and Center for Molecular Medicine, Karolinska Institutet, Stockholm 17177, Sweden.; School of Medical Sciences, Department of Pediatrics, Örebro University and University Hospital, Örebro S-703 62, Sweden., Mao M; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA., Chen A; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA., Skrinar A; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA., Roberts MS; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA., Imel EA; Department of Medicine and Department of Pediatrics, Indiana University School of Medicine, Indianapolis, Indianapolis 46202, USA.
Source: The Journal of clinical endocrinology and metabolism [J Clin Endocrinol Metab] 2022 Jul 14; Vol. 107 (8), pp. e3241-e3253.
Publication Type: Journal Article; Randomized Controlled Trial; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Oxford University Press Country of Publication: United States NLM ID: 0375362 Publication Model: Print Cited Medium: Internet ISSN: 1945-7197 (Electronic) Linking ISSN: 0021972X NLM ISO Abbreviation: J Clin Endocrinol Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia.
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  Data: <searchLink fieldCode="AU" term="%22Ward+LM%22">Ward LM</searchLink>; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario K1H 8L1, Canada.<br /><searchLink fieldCode="AU" term="%22Glorieux+FH%22">Glorieux FH</searchLink>; Shriners Hospitals for Children, Canada, McGill University, Montreal, Quebec H4A OA9, Canada.<br /><searchLink fieldCode="AU" term="%22Whyte+MP%22">Whyte MP</searchLink>; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110,USA.<br /><searchLink fieldCode="AU" term="%22Munns+CF%22">Munns CF</searchLink>; Child Health Research Centre, The University of Queensland, Brisbane, Queensland 4072, Australia.; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland 4101, Australia.<br /><searchLink fieldCode="AU" term="%22Portale+AA%22">Portale AA</searchLink>; Department of Pediatrics, University of California, San Francisco, San Francisco, California 94143, USA.<br /><searchLink fieldCode="AU" term="%22Högler+W%22">Högler W</searchLink>; Department of Pediatrics and Adolescent Medicine, Johannes Kepler University Linz, Linz 4040, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Birmingham, B15 2TT, UK.<br /><searchLink fieldCode="AU" term="%22Simmons+JH%22">Simmons JH</searchLink>; Department of Pediatrics, Division of Endocrinology and Diabetes, Vanderbilt University School of Medicine, Vanderbilt University, 680-8570 Nashville, Tennessee, 63110, USA.<br /><searchLink fieldCode="AU" term="%22Gottesman+GS%22">Gottesman GS</searchLink>; Shriners Hospitals for Children St Louis, St Louis, Missouri 63110, USA.<br /><searchLink fieldCode="AU" term="%22Padidela+R%22">Padidela R</searchLink>; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester M13 9WL, UK.<br /><searchLink fieldCode="AU" term="%22Namba+N%22">Namba N</searchLink>; Department of Pediatrics, Osaka Hospital, Japan.; Community Healthcare Organization.; Osaka University Graduate School of Medicine, Osaka 553-0003, Japan.; Division of Pediatrics and Perinatology, Tottori University Faculty of Medicine, Yonago, Japan.<br /><searchLink fieldCode="AU" term="%22Cheong+HI%22">Cheong HI</searchLink>; Department of Pediatrics, Seoul National University Children's Hospital, Seoul 14068, South Korea.<br /><searchLink fieldCode="AU" term="%22Nilsson+O%22">Nilsson O</searchLink>; Division of Pediatric Endocrinology and Center for Molecular Medicine, Karolinska Institutet, Stockholm 17177, Sweden.; School of Medical Sciences, Department of Pediatrics, Örebro University and University Hospital, Örebro S-703 62, Sweden.<br /><searchLink fieldCode="AU" term="%22Mao+M%22">Mao M</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA.<br /><searchLink fieldCode="AU" term="%22Chen+A%22">Chen A</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA.<br /><searchLink fieldCode="AU" term="%22Skrinar+A%22">Skrinar A</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA.<br /><searchLink fieldCode="AU" term="%22Roberts+MS%22">Roberts MS</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, California 94949, USA.<br /><searchLink fieldCode="AU" term="%22Imel+EA%22">Imel EA</searchLink>; Department of Medicine and Department of Pediatrics, Indiana University School of Medicine, Indianapolis, Indianapolis 46202, USA.
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        Value: 10.1210/clinem/dgac296
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      – TitleFull: Effect of Burosumab Compared With Conventional Therapy on Younger vs Older Children With X-linked Hypophosphatemia.
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