Motor Responses in Pediatric Pompe Disease in the ADVANCE Participant Cohort.

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Title: Motor Responses in Pediatric Pompe Disease in the ADVANCE Participant Cohort.
Authors: Duong T; Department of Neurology, Division of Neuromuscular Medicine, Stanford University School of Medicine, Palo Alto, CA, USA., Kishnani PS; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA., An Haack K; Sanofi, Chilly-Mazarin, France., Foster MC; Sanofi, Cambridge, MA, USA., Gibson JB; Clinical and Metabolic Genetics, Dell Children's Medical Group, Austin, TX, USA., Wilson C; Sanofi, Cambridge, MA, USA., Hahn SH; Departments of Pediatrics and Medicine and Biochemical Genetics Program, Seattle Children's Hospital/University of Washington, Seattle, WA, USA., Hillman R; University of Missouri Child Health, Columbia, MO, USA., Kronn D; Departments of Pathology and Pediatrics, New York Medical College, Valhalla, NY, USA., Leslie ND; Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA., Peña LDM; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.; Current address: Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.; Current address: University of Cincinnati College of Medicine, Cincinnati, OH, USA., Sparks SE; Sanofi, Cambridge, MA, USA., Stockton DW; Division of Genetic, Genomic, and Metabolic Disorders, Central Michigan University and Children's Hospital of Michigan, Detroit, MI, USA., Tanpaiboon P; Rare Disease Institute, Children's National Hospital, Washington, DC, USA.; Current address: Division of Medical Genetics, Child Health Research Center, Torrance, CA, USA., Day JW; Department of Neurology, Division of Neuromuscular Medicine, Stanford University School of Medicine, Palo Alto, CA, USA.
Corporate Authors: Pompe ADVANCE Study Consortium
Source: Journal of neuromuscular diseases [J Neuromuscul Dis] 2022; Vol. 9 (6), pp. 713-730.
Publication Type: Journal Article
Journal Info: Publisher: SAGE Publications Country of Publication: United States NLM ID: 101649948 Publication Model: Print Cited Medium: Internet ISSN: 2214-3602 (Electronic) Linking ISSN: 22143599 NLM ISO Abbreviation: J Neuromuscul Dis Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Motor Responses in Pediatric Pompe Disease in the ADVANCE Participant Cohort.
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  Data: <searchLink fieldCode="AU" term="%22Duong+T%22">Duong T</searchLink>; Department of Neurology, Division of Neuromuscular Medicine, Stanford University School of Medicine, Palo Alto, CA, USA.<br /><searchLink fieldCode="AU" term="%22Kishnani+PS%22">Kishnani PS</searchLink>; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.<br /><searchLink fieldCode="AU" term="%22An+Haack+K%22">An Haack K</searchLink>; Sanofi, Chilly-Mazarin, France.<br /><searchLink fieldCode="AU" term="%22Foster+MC%22">Foster MC</searchLink>; Sanofi, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Gibson+JB%22">Gibson JB</searchLink>; Clinical and Metabolic Genetics, Dell Children's Medical Group, Austin, TX, USA.<br /><searchLink fieldCode="AU" term="%22Wilson+C%22">Wilson C</searchLink>; Sanofi, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Hahn+SH%22">Hahn SH</searchLink>; Departments of Pediatrics and Medicine and Biochemical Genetics Program, Seattle Children's Hospital/University of Washington, Seattle, WA, USA.<br /><searchLink fieldCode="AU" term="%22Hillman+R%22">Hillman R</searchLink>; University of Missouri Child Health, Columbia, MO, USA.<br /><searchLink fieldCode="AU" term="%22Kronn+D%22">Kronn D</searchLink>; Departments of Pathology and Pediatrics, New York Medical College, Valhalla, NY, USA.<br /><searchLink fieldCode="AU" term="%22Leslie+ND%22">Leslie ND</searchLink>; Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.<br /><searchLink fieldCode="AU" term="%22Peña+LDM%22">Peña LDM</searchLink>; Department of Pediatrics, Duke University Medical Center, Durham, NC, USA.; Current address: Division of Human Genetics, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.; Current address: University of Cincinnati College of Medicine, Cincinnati, OH, USA.<br /><searchLink fieldCode="AU" term="%22Sparks+SE%22">Sparks SE</searchLink>; Sanofi, Cambridge, MA, USA.<br /><searchLink fieldCode="AU" term="%22Stockton+DW%22">Stockton DW</searchLink>; Division of Genetic, Genomic, and Metabolic Disorders, Central Michigan University and Children's Hospital of Michigan, Detroit, MI, USA.<br /><searchLink fieldCode="AU" term="%22Tanpaiboon+P%22">Tanpaiboon P</searchLink>; Rare Disease Institute, Children's National Hospital, Washington, DC, USA.; Current address: Division of Medical Genetics, Child Health Research Center, Torrance, CA, USA.<br /><searchLink fieldCode="AU" term="%22Day+JW%22">Day JW</searchLink>; Department of Neurology, Division of Neuromuscular Medicine, Stanford University School of Medicine, Palo Alto, CA, USA.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22SAGE+Publications%22">SAGE Publications </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101649948 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>2214-3602 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2222143599%22">22143599 </searchLink><i>NLM ISO Abbreviation: </i>J Neuromuscul Dis <i>Subsets: </i>MEDLINE
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