Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2.
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| Title: | Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2. |
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| Authors: | Iwayama H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. Electronic address: iwahide1976@gmail.com., Kawahara K; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Takagi M; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Numoto S; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Azuma Y; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Kurahashi H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Yasue Y; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kawajiri H; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Yanase A; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Ito T; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kimura S; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kumagai T; Department of Pediatric Neurology, Aichi Prefectural Colony Central Hospital, Kasugai, Japan; Kuma Home Medical Care Clinic, Nagoya, Japan., Okumura A; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. |
| Source: | Brain & development [Brain Dev] 2023 Feb; Vol. 45 (2), pp. 110-116. Date of Electronic Publication: 2022 Nov 02. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Elsevier Country of Publication: Netherlands NLM ID: 7909235 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1872-7131 (Electronic) Linking ISSN: 03877604 NLM ISO Abbreviation: Brain Dev Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 36335004 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Iwayama+H%22">Iwayama H</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. Electronic address: iwahide1976@gmail.com.<br /><searchLink fieldCode="AU" term="%22Kawahara+K%22">Kawahara K</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Takagi+M%22">Takagi M</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Numoto+S%22">Numoto S</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Azuma+Y%22">Azuma Y</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kurahashi+H%22">Kurahashi H</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Yasue+Y%22">Yasue Y</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kawajiri+H%22">Kawajiri H</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Yanase+A%22">Yanase A</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Ito+T%22">Ito T</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kimura+S%22">Kimura S</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kumagai+T%22">Kumagai T</searchLink>; Department of Pediatric Neurology, Aichi Prefectural Colony Central Hospital, Kasugai, Japan; Kuma Home Medical Care Clinic, Nagoya, Japan.<br /><searchLink fieldCode="AU" term="%22Okumura+A%22">Okumura A</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%227909235%22">Brain & development</searchLink> [Brain Dev] 2023 Feb; Vol. 45 (2), pp. 110-116. <i>Date of Electronic Publication: </i>2022 Nov 02. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier%22">Elsevier </searchLink><i>Country of Publication: </i>Netherlands <i>NLM ID: </i>7909235 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1872-7131 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203877604%22">03877604 </searchLink><i>NLM ISO Abbreviation: </i>Brain Dev <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=36335004 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.braindev.2022.10.006 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 110 Titles: – TitleFull: Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Iwayama H – PersonEntity: Name: NameFull: Kawahara K – PersonEntity: Name: NameFull: Takagi M – PersonEntity: Name: NameFull: Numoto S – PersonEntity: Name: NameFull: Azuma Y – PersonEntity: Name: NameFull: Kurahashi H – PersonEntity: Name: NameFull: Yasue Y – PersonEntity: Name: NameFull: Kawajiri H – PersonEntity: Name: NameFull: Yanase A – PersonEntity: Name: NameFull: Ito T – PersonEntity: Name: NameFull: Kimura S – PersonEntity: Name: NameFull: Kumagai T – PersonEntity: Name: NameFull: Okumura A IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 02 Text: 2023 Feb Type: published Y: 2023 Identifiers: – Type: issn-electronic Value: 1872-7131 Numbering: – Type: volume Value: 45 – Type: issue Value: 2 Titles: – TitleFull: Brain & development Type: main |
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