Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2.

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Title: Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2.
Authors: Iwayama H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. Electronic address: iwahide1976@gmail.com., Kawahara K; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Takagi M; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Numoto S; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Azuma Y; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Kurahashi H; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan., Yasue Y; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kawajiri H; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Yanase A; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Ito T; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kimura S; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan., Kumagai T; Department of Pediatric Neurology, Aichi Prefectural Colony Central Hospital, Kasugai, Japan; Kuma Home Medical Care Clinic, Nagoya, Japan., Okumura A; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
Source: Brain & development [Brain Dev] 2023 Feb; Vol. 45 (2), pp. 110-116. Date of Electronic Publication: 2022 Nov 02.
Publication Type: Journal Article
Journal Info: Publisher: Elsevier Country of Publication: Netherlands NLM ID: 7909235 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1872-7131 (Electronic) Linking ISSN: 03877604 NLM ISO Abbreviation: Brain Dev Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2.
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  Data: <searchLink fieldCode="AU" term="%22Iwayama+H%22">Iwayama H</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan. Electronic address: iwahide1976@gmail.com.<br /><searchLink fieldCode="AU" term="%22Kawahara+K%22">Kawahara K</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Takagi+M%22">Takagi M</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Numoto+S%22">Numoto S</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Azuma+Y%22">Azuma Y</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kurahashi+H%22">Kurahashi H</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Yasue+Y%22">Yasue Y</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kawajiri+H%22">Kawajiri H</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Yanase+A%22">Yanase A</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Ito+T%22">Ito T</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kimura+S%22">Kimura S</searchLink>; Department of Rehabilitation, Aichi Medical University School of Medicine, Nagakute, Japan.<br /><searchLink fieldCode="AU" term="%22Kumagai+T%22">Kumagai T</searchLink>; Department of Pediatric Neurology, Aichi Prefectural Colony Central Hospital, Kasugai, Japan; Kuma Home Medical Care Clinic, Nagoya, Japan.<br /><searchLink fieldCode="AU" term="%22Okumura+A%22">Okumura A</searchLink>; Department of Pediatrics, Aichi Medical University School of Medicine, Nagakute, Japan.
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  Data: <searchLink fieldCode="JN" term="%227909235%22">Brain & development</searchLink> [Brain Dev] 2023 Feb; Vol. 45 (2), pp. 110-116. <i>Date of Electronic Publication: </i>2022 Nov 02.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Elsevier%22">Elsevier </searchLink><i>Country of Publication: </i>Netherlands <i>NLM ID: </i>7909235 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1872-7131 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203877604%22">03877604 </searchLink><i>NLM ISO Abbreviation: </i>Brain Dev <i>Subsets: </i>MEDLINE
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        Value: 10.1016/j.braindev.2022.10.006
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              Text: 2023 Feb
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