Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.

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Title: Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.
Authors: Elsayed MEAA; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kaukonen M; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., Kiraly P; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kapetanovic JC; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., MacLaren RE; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK.
Source: Genes [Genes (Basel)] 2022 Nov 12; Vol. 13 (11). Date of Electronic Publication: 2022 Nov 12.
Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: MDPI Country of Publication: Switzerland NLM ID: 101551097 Publication Model: Electronic Cited Medium: Internet ISSN: 2073-4425 (Electronic) Linking ISSN: 20734425 NLM ISO Abbreviation: Genes (Basel) Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.
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  Data: <searchLink fieldCode="AU" term="%22Elsayed+MEAA%22">Elsayed MEAA</searchLink>; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.<br /><searchLink fieldCode="AU" term="%22Kaukonen+M%22">Kaukonen M</searchLink>; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK.<br /><searchLink fieldCode="AU" term="%22Kiraly+P%22">Kiraly P</searchLink>; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.<br /><searchLink fieldCode="AU" term="%22Kapetanovic+JC%22">Kapetanovic JC</searchLink>; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK.<br /><searchLink fieldCode="AU" term="%22MacLaren+RE%22">MacLaren RE</searchLink>; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK.
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  Data: <searchLink fieldCode="JN" term="%22101551097%22">Genes</searchLink> [Genes (Basel)] 2022 Nov 12; Vol. 13 (11). <i>Date of Electronic Publication: </i>2022 Nov 12.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22MDPI%22">MDPI </searchLink><i>Country of Publication: </i>Switzerland <i>NLM ID: </i>101551097 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2073-4425 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2220734425%22">20734425 </searchLink><i>NLM ISO Abbreviation: </i>Genes (Basel) <i>Subsets: </i>MEDLINE
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        Value: 10.3390/genes13112103
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        Text: English
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              Text: 2022 Nov 12
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              Y: 2022
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