Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.

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Bibliographic Details
Title: Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.
Authors: Elsayed MEAA; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kaukonen M; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., Kiraly P; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kapetanovic JC; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., MacLaren RE; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK.
Source: Genes [Genes (Basel)] 2022 Nov 12; Vol. 13 (11). Date of Electronic Publication: 2022 Nov 12.
Publication Type: Case Reports; Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: MDPI Country of Publication: Switzerland NLM ID: 101551097 Publication Model: Electronic Cited Medium: Internet ISSN: 2073-4425 (Electronic) Linking ISSN: 20734425 NLM ISO Abbreviation: Genes (Basel) Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2073-4425
DOI:10.3390/genes13112103