Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial.

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Title: Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial.
Authors: Miller JL; Department of Pediatric Endocrinology, University of Florida College of Medicine, Gainesville, Florida 32608, USA., Gevers E; Queen Mary University London, London E1 4NS, UK; Barts Health NHS Trust-Royal London Children's Hospital, London E1 1FR, UK., Bridges N; Chelsea and Westminster Hospital, London, UK., Yanovski JA; US Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, Maryland 20892, USA., Salehi P; Endocrinology, Seattle Children's Hospital, Seattle, Washington 98105, USA., Obrynba KS; Endocrinology, Nationwide Children's Hospital, Columbus, Ohio 43205, USA., Felner EI; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia 30322, USA., Bird LM; University of California, San Diego/Rady's Children's Hospital, San Diego, California 92123, USA., Shoemaker AH; Vanderbilt University Medical Center, Nashville, Tennessee 37240, USA., Angulo M; NYU Langone Health, Mineola, New York 11501, USA., Butler MG; University of Kansas Medical Center, Kansas City, Kansas 66160, USA., Stevenson D; Stanford University, Palo Alto, California 94305, USA., Abuzzahab J; Children's Minnesota, Minneapolis, Minnesota 55404, USA., Barrett T; Birmingham Women's and Children's Hospital, Birmingham B15 2TG, UK., Lah M; Indiana University School of Medicine, Indianapolis, Indiana 46202, USA., Littlejohn E; Sparrow Clinical Research Institute, Lansing, Michigan 48912, USA., Mathew V; Hull and East Yorkshire Hospitals NHS Trust, Hull HU3 2JZ, UK., Cowen NM; Soleno Therapeutics, Redwood City, California 94065, USA., Bhatnagar A; Soleno Therapeutics, Redwood City, California 94065, USA.
Corporate Authors: DESTINY PWS Investigators
Source: The Journal of clinical endocrinology and metabolism [J Clin Endocrinol Metab] 2023 Jun 16; Vol. 108 (7), pp. 1676-1685.
Publication Type: Randomized Controlled Trial; Clinical Trial, Phase III; Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Oxford University Press Country of Publication: United States NLM ID: 0375362 Publication Model: Print Cited Medium: Internet ISSN: 1945-7197 (Electronic) Linking ISSN: 0021972X NLM ISO Abbreviation: J Clin Endocrinol Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial.
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  Data: <searchLink fieldCode="AU" term="%22Miller+JL%22">Miller JL</searchLink>; Department of Pediatric Endocrinology, University of Florida College of Medicine, Gainesville, Florida 32608, USA.<br /><searchLink fieldCode="AU" term="%22Gevers+E%22">Gevers E</searchLink>; Queen Mary University London, London E1 4NS, UK; Barts Health NHS Trust-Royal London Children's Hospital, London E1 1FR, UK.<br /><searchLink fieldCode="AU" term="%22Bridges+N%22">Bridges N</searchLink>; Chelsea and Westminster Hospital, London, UK.<br /><searchLink fieldCode="AU" term="%22Yanovski+JA%22">Yanovski JA</searchLink>; US Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, Maryland 20892, USA.<br /><searchLink fieldCode="AU" term="%22Salehi+P%22">Salehi P</searchLink>; Endocrinology, Seattle Children's Hospital, Seattle, Washington 98105, USA.<br /><searchLink fieldCode="AU" term="%22Obrynba+KS%22">Obrynba KS</searchLink>; Endocrinology, Nationwide Children's Hospital, Columbus, Ohio 43205, USA.<br /><searchLink fieldCode="AU" term="%22Felner+EI%22">Felner EI</searchLink>; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia 30322, USA.<br /><searchLink fieldCode="AU" term="%22Bird+LM%22">Bird LM</searchLink>; University of California, San Diego/Rady's Children's Hospital, San Diego, California 92123, USA.<br /><searchLink fieldCode="AU" term="%22Shoemaker+AH%22">Shoemaker AH</searchLink>; Vanderbilt University Medical Center, Nashville, Tennessee 37240, USA.<br /><searchLink fieldCode="AU" term="%22Angulo+M%22">Angulo M</searchLink>; NYU Langone Health, Mineola, New York 11501, USA.<br /><searchLink fieldCode="AU" term="%22Butler+MG%22">Butler MG</searchLink>; University of Kansas Medical Center, Kansas City, Kansas 66160, USA.<br /><searchLink fieldCode="AU" term="%22Stevenson+D%22">Stevenson D</searchLink>; Stanford University, Palo Alto, California 94305, USA.<br /><searchLink fieldCode="AU" term="%22Abuzzahab+J%22">Abuzzahab J</searchLink>; Children's Minnesota, Minneapolis, Minnesota 55404, USA.<br /><searchLink fieldCode="AU" term="%22Barrett+T%22">Barrett T</searchLink>; Birmingham Women's and Children's Hospital, Birmingham B15 2TG, UK.<br /><searchLink fieldCode="AU" term="%22Lah+M%22">Lah M</searchLink>; Indiana University School of Medicine, Indianapolis, Indiana 46202, USA.<br /><searchLink fieldCode="AU" term="%22Littlejohn+E%22">Littlejohn E</searchLink>; Sparrow Clinical Research Institute, Lansing, Michigan 48912, USA.<br /><searchLink fieldCode="AU" term="%22Mathew+V%22">Mathew V</searchLink>; Hull and East Yorkshire Hospitals NHS Trust, Hull HU3 2JZ, UK.<br /><searchLink fieldCode="AU" term="%22Cowen+NM%22">Cowen NM</searchLink>; Soleno Therapeutics, Redwood City, California 94065, USA.<br /><searchLink fieldCode="AU" term="%22Bhatnagar+A%22">Bhatnagar A</searchLink>; Soleno Therapeutics, Redwood City, California 94065, USA.
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  Data: <searchLink fieldCode="JN" term="%220375362%22">The Journal of clinical endocrinology and metabolism</searchLink> [J Clin Endocrinol Metab] 2023 Jun 16; Vol. 108 (7), pp. 1676-1685.
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      – TitleFull: Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial.
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