Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial.
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| Title: | Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial. |
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| Authors: | Miller JL; Department of Pediatric Endocrinology, University of Florida College of Medicine, Gainesville, Florida 32608, USA., Gevers E; Queen Mary University London, London E1 4NS, UK; Barts Health NHS Trust-Royal London Children's Hospital, London E1 1FR, UK., Bridges N; Chelsea and Westminster Hospital, London, UK., Yanovski JA; US Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, Maryland 20892, USA., Salehi P; Endocrinology, Seattle Children's Hospital, Seattle, Washington 98105, USA., Obrynba KS; Endocrinology, Nationwide Children's Hospital, Columbus, Ohio 43205, USA., Felner EI; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia 30322, USA., Bird LM; University of California, San Diego/Rady's Children's Hospital, San Diego, California 92123, USA., Shoemaker AH; Vanderbilt University Medical Center, Nashville, Tennessee 37240, USA., Angulo M; NYU Langone Health, Mineola, New York 11501, USA., Butler MG; University of Kansas Medical Center, Kansas City, Kansas 66160, USA., Stevenson D; Stanford University, Palo Alto, California 94305, USA., Abuzzahab J; Children's Minnesota, Minneapolis, Minnesota 55404, USA., Barrett T; Birmingham Women's and Children's Hospital, Birmingham B15 2TG, UK., Lah M; Indiana University School of Medicine, Indianapolis, Indiana 46202, USA., Littlejohn E; Sparrow Clinical Research Institute, Lansing, Michigan 48912, USA., Mathew V; Hull and East Yorkshire Hospitals NHS Trust, Hull HU3 2JZ, UK., Cowen NM; Soleno Therapeutics, Redwood City, California 94065, USA., Bhatnagar A; Soleno Therapeutics, Redwood City, California 94065, USA. |
| Corporate Authors: | DESTINY PWS Investigators |
| Source: | The Journal of clinical endocrinology and metabolism [J Clin Endocrinol Metab] 2023 Jun 16; Vol. 108 (7), pp. 1676-1685. |
| Publication Type: | Randomized Controlled Trial; Clinical Trial, Phase III; Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Oxford University Press Country of Publication: United States NLM ID: 0375362 Publication Model: Print Cited Medium: Internet ISSN: 1945-7197 (Electronic) Linking ISSN: 0021972X NLM ISO Abbreviation: J Clin Endocrinol Metab Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 36639249 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Miller+JL%22">Miller JL</searchLink>; Department of Pediatric Endocrinology, University of Florida College of Medicine, Gainesville, Florida 32608, USA.<br /><searchLink fieldCode="AU" term="%22Gevers+E%22">Gevers E</searchLink>; Queen Mary University London, London E1 4NS, UK; Barts Health NHS Trust-Royal London Children's Hospital, London E1 1FR, UK.<br /><searchLink fieldCode="AU" term="%22Bridges+N%22">Bridges N</searchLink>; Chelsea and Westminster Hospital, London, UK.<br /><searchLink fieldCode="AU" term="%22Yanovski+JA%22">Yanovski JA</searchLink>; US Eunice Kennedy Shriver National Institute of Child Health and Human Development, National Institutes of Health, Bethesda, Maryland 20892, USA.<br /><searchLink fieldCode="AU" term="%22Salehi+P%22">Salehi P</searchLink>; Endocrinology, Seattle Children's Hospital, Seattle, Washington 98105, USA.<br /><searchLink fieldCode="AU" term="%22Obrynba+KS%22">Obrynba KS</searchLink>; Endocrinology, Nationwide Children's Hospital, Columbus, Ohio 43205, USA.<br /><searchLink fieldCode="AU" term="%22Felner+EI%22">Felner EI</searchLink>; Department of Pediatrics, Emory University School of Medicine, Atlanta, Georgia 30322, USA.<br /><searchLink fieldCode="AU" term="%22Bird+LM%22">Bird LM</searchLink>; University of California, San Diego/Rady's Children's Hospital, San Diego, California 92123, USA.<br /><searchLink fieldCode="AU" term="%22Shoemaker+AH%22">Shoemaker AH</searchLink>; Vanderbilt University Medical Center, Nashville, Tennessee 37240, USA.<br /><searchLink fieldCode="AU" term="%22Angulo+M%22">Angulo M</searchLink>; NYU Langone Health, Mineola, New York 11501, USA.<br /><searchLink fieldCode="AU" term="%22Butler+MG%22">Butler MG</searchLink>; University of Kansas Medical Center, Kansas City, Kansas 66160, USA.<br /><searchLink fieldCode="AU" term="%22Stevenson+D%22">Stevenson D</searchLink>; Stanford University, Palo Alto, California 94305, USA.<br /><searchLink fieldCode="AU" term="%22Abuzzahab+J%22">Abuzzahab J</searchLink>; Children's Minnesota, Minneapolis, Minnesota 55404, USA.<br /><searchLink fieldCode="AU" term="%22Barrett+T%22">Barrett T</searchLink>; Birmingham Women's and Children's Hospital, Birmingham B15 2TG, UK.<br /><searchLink fieldCode="AU" term="%22Lah+M%22">Lah M</searchLink>; Indiana University School of Medicine, Indianapolis, Indiana 46202, USA.<br /><searchLink fieldCode="AU" term="%22Littlejohn+E%22">Littlejohn E</searchLink>; Sparrow Clinical Research Institute, Lansing, Michigan 48912, USA.<br /><searchLink fieldCode="AU" term="%22Mathew+V%22">Mathew V</searchLink>; Hull and East Yorkshire Hospitals NHS Trust, Hull HU3 2JZ, UK.<br /><searchLink fieldCode="AU" term="%22Cowen+NM%22">Cowen NM</searchLink>; Soleno Therapeutics, Redwood City, California 94065, USA.<br /><searchLink fieldCode="AU" term="%22Bhatnagar+A%22">Bhatnagar A</searchLink>; Soleno Therapeutics, Redwood City, California 94065, USA. – Name: AuthorCorporate Label: Corporate Authors Group: Au Data: <searchLink fieldCode="CA" term="%22DESTINY+PWS+Investigators%22">DESTINY PWS Investigators</searchLink> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%220375362%22">The Journal of clinical endocrinology and metabolism</searchLink> [J Clin Endocrinol Metab] 2023 Jun 16; Vol. 108 (7), pp. 1676-1685. – Name: TypePub Label: Publication Type Group: TypPub Data: Randomized Controlled Trial; Clinical Trial, Phase III; Journal Article; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0375362 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1945-7197 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%220021972X%22">0021972X </searchLink><i>NLM ISO Abbreviation: </i>J Clin Endocrinol Metab <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=36639249 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1210/clinem/dgad014 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 1676 Titles: – TitleFull: Diazoxide Choline Extended-Release Tablet in People With Prader-Willi Syndrome: A Double-Blind, Placebo-Controlled Trial. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Miller JL – PersonEntity: Name: NameFull: Gevers E – PersonEntity: Name: NameFull: Bridges N – PersonEntity: Name: NameFull: Yanovski JA – PersonEntity: Name: NameFull: Salehi P – PersonEntity: Name: NameFull: Obrynba KS – PersonEntity: Name: NameFull: Felner EI – PersonEntity: Name: NameFull: Bird LM – PersonEntity: Name: NameFull: Shoemaker AH – PersonEntity: Name: NameFull: Angulo M – PersonEntity: Name: NameFull: Butler MG – PersonEntity: Name: NameFull: Stevenson D – PersonEntity: Name: NameFull: Abuzzahab J – PersonEntity: Name: NameFull: Barrett T – PersonEntity: Name: NameFull: Lah M – PersonEntity: Name: NameFull: Littlejohn E – PersonEntity: Name: NameFull: Mathew V – PersonEntity: Name: NameFull: Cowen NM – PersonEntity: Name: NameFull: Bhatnagar A IsPartOfRelationships: – BibEntity: Dates: – D: 16 M: 06 Text: 2023 Jun 16 Type: published Y: 2023 Identifiers: – Type: issn-electronic Value: 1945-7197 Numbering: – Type: volume Value: 108 – Type: issue Value: 7 Titles: – TitleFull: The Journal of clinical endocrinology and metabolism Type: main |
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