Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level.

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Title: Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level.
Authors: Imel EA; Departments of Medicine and Pediatrics, Indiana University School of Medicine, Indianapolis, IN 46202, USA., Glorieux FH; Emeritus Director of Research, Shriners Hospitals for Children-Canada, Montreal, QC H4A 0A9, Canada., Whyte MP; Center for Metabolic Bone Disease and Molecular Research, Shriners Hospitals for Children-St. Louis, St Louis, MO 63110, USA., Portale AA; Department of Pediatrics, University of California, San Francisco, San Francisco, CA 94115, USA., Munns CF; The University of Queensland, Queensland Children's Hospital, South Brisbane, QLD 4101, Australia., Nilsson O; Division of Pediatric Endocrinology and Center for Molecular Medicine, Department of Women's and Children's Health, Karolinska Institutet and University Hospital, Stockholm 171 64, Sweden.; School of Medical Sciences and Department of Pediatrics, Örebro University and University Hospital, Örebro 701 85, Sweden., Simmons JH; Department of Pediatrics, Vanderbilt University Medical Center, Nashville, TN 37232, USA., Padidela R; Paediatric Endocrinology, Royal Manchester Children's Hospital and Faculty of Biology, Medicine and Health, University of Manchester, Manchester M13 9PL, UK., Namba N; Department of Pediatrics, Osaka Hospital, Japan Community Healthcare Organization, Osaka 553-0003, Japan.; Department of Pediatrics, Osaka University Graduate School of Medicine, Suita 565-0871, Japan., Cheong HI; Department of Pediatrics, Hallym University Sacred Heart Hospital, Anyang-si, Gyeonggi-do, South Korea., Pitukcheewanont P; Children's Hospital Los Angeles, Los Angeles, CA and Keck School of Medicine of USC, Los Angeles, CA 90027, USA., Sochett E; Department of Endocrinology, The Hospital for Sick Children, Toronto, ON M5G 1X8, Canada., Högler W; Department of Pediatrics and Adolescent Medicine, Johannes Kepler University Linz, Linz 4040, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Birmingham B15 2TT, UK., Muroya K; Kanagawa Children's Medical Center, Yokohama 232-0066, Japan., Tanaka H; Okayama Saiseikai General Hospital, Okayama 700-0021, Japan., Gottesman GS; Center for Metabolic Bone Disease and Molecular Research, Shriners Hospitals for Children-St. Louis, St Louis, MO 63110, USA.; Washington University School of Medicine, St Louis, MO 63110, USA., Biggin A; Children's Hospital Westmead, Westmead 2145, Australia., Perwad F; Department of Pediatrics, University of California, San Francisco, San Francisco, CA 94115, USA., Chen A; Ultragenyx Pharmaceutical Inc, Novato, CA 94949, USA., Roberts MS; Ultragenyx Pharmaceutical Inc, Novato, CA 94949, USA., Ward LM; Department of Pediatrics, University of Ottawa, Children's Hospital of Eastern Ontario, Ottawa, Ontario K1H 8L1, Canada.
Source: The Journal of clinical endocrinology and metabolism [J Clin Endocrinol Metab] 2023 Oct 18; Vol. 108 (11), pp. 2990-2998.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Oxford University Press Country of Publication: United States NLM ID: 0375362 Publication Model: Print Cited Medium: Internet ISSN: 1945-7197 (Electronic) Linking ISSN: 0021972X NLM ISO Abbreviation: J Clin Endocrinol Metab Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Burosumab vs Phosphate/Active Vitamin D in Pediatric X-Linked Hypophosphatemia: A Subgroup Analysis by Dose Level.
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  Data: <searchLink fieldCode="AU" term="%22Imel+EA%22">Imel EA</searchLink>; Departments of Medicine and Pediatrics, Indiana University School of Medicine, Indianapolis, IN 46202, USA.<br /><searchLink fieldCode="AU" term="%22Glorieux+FH%22">Glorieux FH</searchLink>; Emeritus Director of Research, Shriners Hospitals for Children-Canada, Montreal, QC H4A 0A9, Canada.<br /><searchLink fieldCode="AU" term="%22Whyte+MP%22">Whyte MP</searchLink>; Center for Metabolic Bone Disease and Molecular Research, Shriners Hospitals for Children-St. Louis, St Louis, MO 63110, USA.<br /><searchLink fieldCode="AU" term="%22Portale+AA%22">Portale AA</searchLink>; Department of Pediatrics, University of California, San Francisco, San Francisco, CA 94115, USA.<br /><searchLink fieldCode="AU" term="%22Munns+CF%22">Munns CF</searchLink>; The University of Queensland, Queensland Children's Hospital, South Brisbane, QLD 4101, Australia.<br /><searchLink fieldCode="AU" term="%22Nilsson+O%22">Nilsson O</searchLink>; Division of Pediatric Endocrinology and Center for Molecular Medicine, Department of Women's and Children's Health, Karolinska Institutet and University Hospital, Stockholm 171 64, Sweden.; School of Medical Sciences and Department of Pediatrics, Örebro University and University Hospital, Örebro 701 85, Sweden.<br /><searchLink fieldCode="AU" term="%22Simmons+JH%22">Simmons JH</searchLink>; Department of Pediatrics, Vanderbilt University Medical Center, Nashville, TN 37232, USA.<br /><searchLink fieldCode="AU" term="%22Padidela+R%22">Padidela R</searchLink>; Paediatric Endocrinology, Royal Manchester Children's Hospital and Faculty of Biology, Medicine and Health, University of Manchester, Manchester M13 9PL, UK.<br /><searchLink fieldCode="AU" term="%22Namba+N%22">Namba N</searchLink>; Department of Pediatrics, Osaka Hospital, Japan Community Healthcare Organization, Osaka 553-0003, Japan.; Department of Pediatrics, Osaka University Graduate School of Medicine, Suita 565-0871, Japan.<br /><searchLink fieldCode="AU" term="%22Cheong+HI%22">Cheong HI</searchLink>; Department of Pediatrics, Hallym University Sacred Heart Hospital, Anyang-si, Gyeonggi-do, South Korea.<br /><searchLink fieldCode="AU" term="%22Pitukcheewanont+P%22">Pitukcheewanont P</searchLink>; Children's Hospital Los Angeles, Los Angeles, CA and Keck School of Medicine of USC, Los Angeles, CA 90027, USA.<br /><searchLink fieldCode="AU" term="%22Sochett+E%22">Sochett E</searchLink>; Department of Endocrinology, The Hospital for Sick Children, Toronto, ON M5G 1X8, Canada.<br /><searchLink fieldCode="AU" term="%22Högler+W%22">Högler W</searchLink>; Department of Pediatrics and Adolescent Medicine, Johannes Kepler University Linz, Linz 4040, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Birmingham B15 2TT, UK.<br /><searchLink fieldCode="AU" term="%22Muroya+K%22">Muroya K</searchLink>; Kanagawa Children's Medical Center, Yokohama 232-0066, Japan.<br /><searchLink fieldCode="AU" term="%22Tanaka+H%22">Tanaka H</searchLink>; Okayama Saiseikai General Hospital, Okayama 700-0021, Japan.<br /><searchLink fieldCode="AU" term="%22Gottesman+GS%22">Gottesman GS</searchLink>; Center for Metabolic Bone Disease and Molecular Research, Shriners Hospitals for Children-St. Louis, St Louis, MO 63110, USA.; Washington University School of Medicine, St Louis, MO 63110, USA.<br /><searchLink fieldCode="AU" term="%22Biggin+A%22">Biggin A</searchLink>; Children's Hospital Westmead, Westmead 2145, Australia.<br /><searchLink fieldCode="AU" term="%22Perwad+F%22">Perwad F</searchLink>; Department of Pediatrics, University of California, San Francisco, San Francisco, CA 94115, USA.<br /><searchLink fieldCode="AU" term="%22Chen+A%22">Chen A</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, CA 94949, USA.<br /><searchLink fieldCode="AU" term="%22Roberts+MS%22">Roberts MS</searchLink>; Ultragenyx Pharmaceutical Inc, Novato, CA 94949, USA.<br /><searchLink fieldCode="AU" term="%22Ward+LM%22">Ward LM</searchLink>; Department of Pediatrics, University of Ottawa, Children's Hospital of Eastern Ontario, Ottawa, Ontario K1H 8L1, Canada.
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  Data: <searchLink fieldCode="JN" term="%220375362%22">The Journal of clinical endocrinology and metabolism</searchLink> [J Clin Endocrinol Metab] 2023 Oct 18; Vol. 108 (11), pp. 2990-2998.
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