Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach.
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| Title: | Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach. |
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| Authors: | Centa JL; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL 60064, USA., Stratton MP; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL 60064, USA.; School of Graduate and Postdoctoral Studies, Rosalind Franklin University of Medicine and Science, North Chicago, IL 60064, USA., Pratt MA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Osterlund Oltmanns JR; Department of Psychology, Northern Illinois University, DeKalb, IL 60115, USA., Wallace DG; Department of Psychology, Northern Illinois University, DeKalb, IL 60115, USA., Miller SA; Psychology Department, College of Health Professionals, Rosalind Franklin University of Medicine and Science, North Chicago, IL 60064, USA., Weimer JM; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA.; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD 57104, USA., Hastings ML; Center for Genetic Diseases, Chicago Medical School, Rosalind Franklin University of Medicine and Science, North Chicago, IL 60064, USA.; Department of Pharmacology, University of Michigan Medical School, Ann Arbor, MI 48109, USA. |
| Source: | Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2023 Jun 03; Vol. 33, pp. 15-27. Date of Electronic Publication: 2023 Jun 03 (Print Publication: 2023). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
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