View in EDS

Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C.

Saved in:
Bibliographic Details
Title: Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C.
Authors: Martinez-Navajas G; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain., Ceron-Hernandez J; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain., Simon I; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain., Lupiañez P; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain., Diaz-McLynn S; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain., Perales S; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.; Instituto de Investigación Biosanitaria Ibs.GRANADA, Granada, Spain., Modlich U; Department of Gene and Cell Therapy, Institute of Regenerative Medicine, University of Zürich, Wagistrasse 12, 8952 Schlieren-Zürich, Switzerland., Guerrero JA; Department of Haematology, University of Cambridge, Cambridge, UK.; National Health Service Blood and Transplant, Cambridge Biomedical Campus, Cambridge, UK., Martin F; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology III and Immunology, Faculty of Medicine, Avenida Ilustracion S/n, 18016 Granada, Spain., Sevivas T; Serviço de Sangue, Medicina Transfusional e Imunohemoterapia Do Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal., Lozano ML; Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII, U765 Murcia, Spain., Rivera J; Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII, U765 Murcia, Spain.; Grupo Español de Alteraciones Plaquetarias Congénitas (GEAPC), Madrid, Spain., Ramos-Mejia V; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain., Tersteeg C; Laboratory for Thrombosis Research, IRF Life Sciences, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium., Real PJ; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.; Instituto de Investigación Biosanitaria Ibs.GRANADA, Granada, Spain.
Source: Molecular therapy. Nucleic acids [Mol Ther Nucleic Acids] 2023 Jun 12; Vol. 33, pp. 75-92. Date of Electronic Publication: 2023 Jun 12 (Print Publication: 2023).
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101581621 Publication Model: eCollection Cited Medium: Print ISSN: 2162-2531 (Print) Linking ISSN: 21622531 NLM ISO Abbreviation: Mol Ther Nucleic Acids Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 37416759
AccessLevel: 2
PubType: Academic Journal
PubTypeId: academicJournal
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Martinez-Navajas+G%22">Martinez-Navajas G</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Ceron-Hernandez+J%22">Ceron-Hernandez J</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Simon+I%22">Simon I</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Lupiañez+P%22">Lupiañez P</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Diaz-McLynn+S%22">Diaz-McLynn S</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Perales+S%22">Perales S</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.; Instituto de Investigación Biosanitaria Ibs.GRANADA, Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Modlich+U%22">Modlich U</searchLink>; Department of Gene and Cell Therapy, Institute of Regenerative Medicine, University of Zürich, Wagistrasse 12, 8952 Schlieren-Zürich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Guerrero+JA%22">Guerrero JA</searchLink>; Department of Haematology, University of Cambridge, Cambridge, UK.; National Health Service Blood and Transplant, Cambridge Biomedical Campus, Cambridge, UK.<br /><searchLink fieldCode="AU" term="%22Martin+F%22">Martin F</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology III and Immunology, Faculty of Medicine, Avenida Ilustracion S/n, 18016 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Sevivas+T%22">Sevivas T</searchLink>; Serviço de Sangue, Medicina Transfusional e Imunohemoterapia Do Centro Hospitalar e Universitário de Coimbra, Coimbra, Portugal.<br /><searchLink fieldCode="AU" term="%22Lozano+ML%22">Lozano ML</searchLink>; Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII, U765 Murcia, Spain.<br /><searchLink fieldCode="AU" term="%22Rivera+J%22">Rivera J</searchLink>; Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER-ISCIII, U765 Murcia, Spain.; Grupo Español de Alteraciones Plaquetarias Congénitas (GEAPC), Madrid, Spain.<br /><searchLink fieldCode="AU" term="%22Ramos-Mejia+V%22">Ramos-Mejia V</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.<br /><searchLink fieldCode="AU" term="%22Tersteeg+C%22">Tersteeg C</searchLink>; Laboratory for Thrombosis Research, IRF Life Sciences, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium.<br /><searchLink fieldCode="AU" term="%22Real+PJ%22">Real PJ</searchLink>; GENyO, Pfizer-Universidad de Granada-Junta de Andalucia Centre for Genomics and Oncological Research, PTS, Granada, Avenida de la Ilustracion 114, 18016 Granada, Spain.; University of Granada, Department of Biochemistry and Molecular Biology I, Faculty of Science, Avenida Fuentenueva S/n, 18071 Granada, Spain.; Instituto de Investigación Biosanitaria Ibs.GRANADA, Granada, Spain.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%22101581621%22">Molecular therapy. Nucleic acids</searchLink> [Mol Ther Nucleic Acids] 2023 Jun 12; Vol. 33, pp. 75-92. <i>Date of Electronic Publication: </i>2023 Jun 12 (<i>Print Publication: </i>2023).
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Journal Article
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101581621 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Print <i>ISSN: </i>2162-2531 (Print) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2221622531%22">21622531 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther Nucleic Acids <i>Subsets: </i>PubMed not MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=37416759
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1016/j.omtn.2023.06.008
    Languages:
      – Code: eng
        Text: English
    PhysicalDescription:
      Pagination:
        StartPage: 75
    Titles:
      – TitleFull: Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Martinez-Navajas G
      – PersonEntity:
          Name:
            NameFull: Ceron-Hernandez J
      – PersonEntity:
          Name:
            NameFull: Simon I
      – PersonEntity:
          Name:
            NameFull: Lupiañez P
      – PersonEntity:
          Name:
            NameFull: Diaz-McLynn S
      – PersonEntity:
          Name:
            NameFull: Perales S
      – PersonEntity:
          Name:
            NameFull: Modlich U
      – PersonEntity:
          Name:
            NameFull: Guerrero JA
      – PersonEntity:
          Name:
            NameFull: Martin F
      – PersonEntity:
          Name:
            NameFull: Sevivas T
      – PersonEntity:
          Name:
            NameFull: Lozano ML
      – PersonEntity:
          Name:
            NameFull: Rivera J
      – PersonEntity:
          Name:
            NameFull: Ramos-Mejia V
      – PersonEntity:
          Name:
            NameFull: Tersteeg C
      – PersonEntity:
          Name:
            NameFull: Real PJ
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 12
              M: 06
              Text: 2023 Jun 12
              Type: published
              Y: 2023
          Identifiers:
            – Type: issn-print
              Value: 2162-2531
          Numbering:
            – Type: volume
              Value: 33
          Titles:
            – TitleFull: Molecular therapy. Nucleic acids
              Type: main
ResultId 1