Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C. - Martinez-Navajas G; Ceron-Hernandez J; Simon I; Lupiañez P; Diaz-McLynn S; Perales S; Modlich U; Guerrero JA; Martin F; Sevivas T; Lozano ML; Rivera J; et al. (Molecular therapy. Nucleic acids, 2023)