Comparative Effectiveness of Autologous Hematopoietic Stem Cell Transplant vs Fingolimod, Natalizumab, and Ocrelizumab in Highly Active Relapsing-Remitting Multiple Sclerosis.

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Title: Comparative Effectiveness of Autologous Hematopoietic Stem Cell Transplant vs Fingolimod, Natalizumab, and Ocrelizumab in Highly Active Relapsing-Remitting Multiple Sclerosis.
Authors: Kalincik T; Neuroimmunology Centre, Department of Neurology, Royal Melbourne Hospital, Melbourne, Victoria, Australia.; CORe, Department of Medicine, University of Melbourne, Melbourne, Victoria, Australia., Sharmin S; Neuroimmunology Centre, Department of Neurology, Royal Melbourne Hospital, Melbourne, Victoria, Australia.; CORe, Department of Medicine, University of Melbourne, Melbourne, Victoria, Australia., Roos I; Neuroimmunology Centre, Department of Neurology, Royal Melbourne Hospital, Melbourne, Victoria, Australia.; CORe, Department of Medicine, University of Melbourne, Melbourne, Victoria, Australia., Freedman MS; University of Ottawa, Department of Medicine, Ottawa Hospital Research Institute, Ottawa, Ontario, Canada., Atkins H; Ottawa Hospital Research Institute, University of Ottawa, Ottawa, Ontario, Canada., Burman J; Department of Medical Sciences, Neurology, Uppsala University, Uppsala, Sweden., Massey J; Department of Neurology, St Vincent's Hospital Sydney, Sydney, New South Wales, Australia.; St Vincent's Clinical School, University of New South Wales, Sydney, New South Wales, Australia., Sutton I; Department of Neurology, St Vincent's Hospital Sydney, Sydney, New South Wales, Australia.; University of Sydney, Sydney, New South Wales, Australia., Withers B; St Vincent's Clinical School, University of New South Wales, Sydney, New South Wales, Australia.; Department of Haematology, St Vincent's Hospital Sydney, Sydney, New South Wales, Australia., Macdonell R; Department of Neurology, Austin Health, Melbourne, Victoria, Australia.; University of Melbourne, Melbourne, Victoria, Australia., Grigg A; University of Melbourne, Melbourne, Victoria, Australia.; Department of Haematology, Austin Health, Melbourne, Victoria, Australia., Torkildsen Ø; Department of Neurology, Haukeland University Hospital, Bergen, Norway., Bo L; Department of Neurology, Haukeland University Hospital, Bergen, Norway., Lehmann AK; Department of Haematology, Haukeland University Hospital, Bergen, Norway., Havrdova EK; Department of Neurology and Center of Clinical Neuroscience, First Faculty of Medicine, Charles University in Prague and General University Hospital, Prague, Czech Republic., Krasulova E; Department of Neurology and Center of Clinical Neuroscience, First Faculty of Medicine, Charles University in Prague and General University Hospital, Prague, Czech Republic., Trnený M; Department of Haematology, First Faculty of Medicine, Charles University in Prague and General University Hospital, Prague, Czech Republic., Kozak T; Department of Haematology, 3rd Faculty of Medicine, Charles University in Prague, and University Hospital Kralovske Vinohrady, Prague, Czech Republic., van der Walt A; Department of Neurology, The Alfred Hospital, Melbourne, Victoria, Australia.; Central Clinical School, Monash University, Melbourne, Victoria, Australia., Butzkueven H; Department of Neurology, The Alfred Hospital, Melbourne, Victoria, Australia.; Central Clinical School, Monash University, Melbourne, Victoria, Australia., McCombe P; University of Queensland, Brisbane, Queensland, Australia.; Royal Brisbane and Women's Hospital, Brisbane, Queensland, Australia., Skibina O; Department of Neurology, The Alfred Hospital, Melbourne, Victoria, Australia.; Department of Neurology, Box Hill Hospital, Melbourne, Victoria, Australia.; Monash University, Melbourne, Victoria, Australia., Lechner-Scott J; School of Medicine and Public Health, University Newcastle, Newcastle, New South Wales, Australia.; Department of Neurology, John Hunter Hospital, Hunter New England Health, Newcastle, New South Wales, Australia., Willekens B; Department of Neurology, Antwerp University Hospital, Edegem, Belgium.; Translational Neurosciences Research Group, Faculty of Medicine and Health Sciences, University of Antwerp, Wilrijk, Belgium., Cartechini E; UOC Neurologia, Azienda Sanitaria Unica Regionale Marche-AV3, Macerata, Italy., Ozakbas S; Dokuz Eylul University, Konak, Izmir, Turkey., Alroughani R; Division of Neurology, Department of Medicine, Amiri Hospital, Sharq, Kuwait., Kuhle J; Neurologic Clinic and Policlinic, Departments of Medicine and Clinical Research, University Hospital and University of Basel, Basel, Switzerland., Patti F; Department of Medical and Surgical Sciences and Advanced Technologies, GF Ingrassia, Catania, Italy.; Multiple Sclerosis Center, University of Catania, Catania, Italy., Duquette P; CHUM MS Center and Universite de Montreal, Montreal, Quebec, Canada., Lugaresi A; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.; Dipartimento di Scienze Biomediche e Neuromotorie, Università di Bologna, Bologna, Italy., Khoury SJ; Nehme and Therese Tohme Multiple Sclerosis Center, American University of Beirut Medical Center, Beirut, Lebanon., Slee M; Flinders University, Adelaide, South Australia, Australia., Turkoglu R; Haydarpasa Numune Training and Research Hospital, Istanbul, Turkey., Hodgkinson S; Liverpool Hospital, Sydney, New South Wales, Australia., John N; Monash Medical Centre, Melbourne, Victoria, Australia.; Department of Medicine, School of Clinical Sciences, Monash University, Melbourne, Victoria, Australia., Maimone D; Garibaldi Hospital, Catania, Italy., Sa MJ; Department of Neurology, Centro Hospitalar Universitario de Sao Joao, Porto, Portugal., van Pesch V; Cliniques Universitaires Saint-Luc, Brussels, Belgium.; Université Catholique de Louvain, Ottignies-Louvain-la-Neuve, Belgium., Gerlach O; Academic MS Center Zuyderland, Department of Neurology, Zuyderland Medical Center, Sittard-Geleen, the Netherlands.; School for Mental Health and Neuroscience, Maastricht University, Maastricht, the Netherlands., Laureys G; Department of Neurology, University Hospital Ghent, Ghent, Belgium., Van Hijfte L; Department of Neurology, University Hospital Ghent, Ghent, Belgium., Karabudak R; Department of Neurology, Hacettepe University Hospitals, Ankara, Turkey., Spitaleri D; Azienda Ospedaliera di Rilievo Nazionale San Giuseppe Moscati Avellino, Avellino, Italy., Csepany T; Department of Neurology, Faculty of Medicine, University of Debrecen, Debrecen, Hungary., Gouider R; Department of Neurology, Razi University Hospital, Manouba, Tunis, Tunisia.; Faculty of Medicine of Tunis, University of Tunis El Manar, Tunis, Tunisia., Castillo-Triviño T; Hospital Universitario Donostia, San Sebastián, Spain., Taylor B; Menzies Institute for Medical Research, University of Tasmania, Hobart, Tasmania, Australia.; Royal Hobart Hospital, Hobart, Tasmania, Australia., Sharrack B; Department of Neurology, Sheffield Teaching Hospitals NHS Foundation Trust, Sheffield, United Kingdom., Snowden JA; Department of Haematology, Sheffield Teaching Hospitals NHS Foundation Trust, Sheffield, United Kingdom., Mrabet S; Department of Neurology, Razi University Hospital, Manouba, Tunis, Tunisia.; Faculty of Medicine of Tunis, University of Tunis El Manar, Tunis, Tunisia., Garber J; Westmead Hospital, Sydney, New South Wales, Australia., Sanchez-Menoyo JL; Hospital de Galdakao-Usansolo, Galdakao, Spain., Aguera-Morales E; University Hospital Reina Sofia, Cordoba, Spain., Blanco Y; Center of Neuroimmunology, Service of Neurology, Hospital Clinic de Barcelona, Barcelona, Spain., Al-Asmi A; Department of Medicine, Sultan Qaboos University Hospital, Al-Khodh, Oman., Weinstock-Guttman B; Department of Neurology, Buffalo General Medical Center, Buffalo, New York., Fragoso Y; Universidade Metropolitana de Santos, Santos, Brazil., de Gans K; Groene Hart Ziekenhuis, Gouda, the Netherlands., Kermode A; Perron Institute, University of Western Australia, Nedlands, Western Australia, Australia.; Institute of Immunology and Infectious Diseases, Sir Charles Gairdner Hospital, Murdoch University, Perth, Western Australia, Australia.
Corporate Authors: MSBase Study Group Collaborators, MSBase Study Group Authors, MSBase Study Group
Source: JAMA neurology [JAMA Neurol] 2023 Jul 01; Vol. 80 (7), pp. 702-713.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: American Medical Association Country of Publication: United States NLM ID: 101589536 Publication Model: Print Cited Medium: Internet ISSN: 2168-6157 (Electronic) Linking ISSN: 21686149 NLM ISO Abbreviation: JAMA Neurol Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:2168-6157
DOI:10.1001/jamaneurol.2023.1184